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Proceedings of the National Academy of Sciences of the United States of America

Volumn 99, Issue 9, 2002, Pages 5760-5762

Brain-directed gene therapy for lysosomal storage disease: Going well beyond the blood-brain barrier

(2) Sly, William S a Vogler, Carole a

a SAINT LOUIS UNIVERSITY SCHOOL OF MEDICINE (United States)

Author keywords

[No Author keywords available]

Indexed keywords

BETA GLUCURONIDASE; GLOBOTRIAOSYLCERAMIDE; GLYCOSPHINGOLIPID; LEVO IDURONIDASE; N ACETYLGALACTOSAMINE 4 SULFATASE; SPHINGOLIPID;

ANIMAL EXPERIMENT; ANIMAL MODEL; BLOOD BRAIN BARRIER; CLINICAL TRIAL; CONTROLLED CLINICAL TRIAL; CONTROLLED STUDY; DRUG ACTIVITY; ENZYME REPLACEMENT; GAUCHER DISEASE; GENE THERAPY; HUMAN; LYSOSOME; LYSOSOME STORAGE DISEASE; NONHUMAN; NOTE; PRIORITY JOURNAL;

ANIMALS; BLOOD-BRAIN BARRIER; CENTRAL NERVOUS SYSTEM DISEASES; GENE THERAPY; HUMANS; LYSOSOMAL STORAGE DISEASES; LYSOSOMES; MICE; MUCOPOLYSACCHARIDOSIS VII;

ANIMALIA;

EID: 0037197831 PISSN: 00278424 EISSN: None Source Type: Journal
DOI: 10.1073/pnas.102175599 Document Type: Note

Times cited : (45)

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