Murine mucopolysaccharidosis type VII: Long term therapeutic effects of enzyme replacement and enzyme replacement followed by bone marrow transplantation

Journal of Clinical Investigation

Volumn 99, Issue 7, 1997, Pages 1596-1605

  Sands, Mark S ^a   Vogler, Carole ^b   Torrey, Aletha ^c   Levy, Beth ^b   Gwynn, Babette ^c   Grubb, Jeff ^b   Sly, William S ^b   Birkenmeier, Edward H ^c  

^a WASHINGTON UNIVERSITY SCHOOL OF MEDICINE   (United States)

^b SAINT LOUIS UNIVERSITY SCHOOL OF MEDICINE   (United States)

^c JACKSON LABORATORY   (United States)

Author keywords

animal models; central nervous system; lysosomal storage diseases; Sly syndrome; glucuronidase

Indexed keywords

BETA GLUCURONIDASE;

ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; BONE MARROW TRANSPLANTATION; CONTROLLED STUDY; ENZYME ACTIVITY; ENZYME LOCALIZATION; ENZYME RECONSTITUTION; LIVER; MOUSE; MUCOPOLYSACCHARIDOSIS TYPE 7; NONHUMAN; PRIORITY JOURNAL; SPLEEN; TISSUE DISTRIBUTION;

EID: 0030898926     PISSN: 00219738     EISSN: None     Source Type: Journal    
DOI: 10.1172/JCI119322     Document Type: Article

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