Molecular pathophysiology and targeted therapeutics for muscular dystrophy

Trends in Pharmacological Sciences

Volumn 22, Issue 9, 2001, Pages 465-470

  Hoffman, Eric P ^a   Dressman, Devin ^a  

^a CHILDREN'S NATIONAL MEDICAL CENTER   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

CLENBUTEROL; CORTICOSTEROID; CREATININE; DEFLAZACORT; DYSTROPHIN; GENTAMICIN; GLUTAMINE; PENTOXIFYLLINE; PREDNISONE; UTROPHIN; VIRUS VECTOR;

ADENO ASSOCIATED VIRUS; BECKER MUSCULAR DYSTROPHY; CELL TRANSPLANTATION; CLINICAL TRIAL; DOG; DRUG TARGETING; DUCHENNE MUSCULAR DYSTROPHY; EXON; GENE MUTATION; GENE TARGETING; HUMAN; NONHUMAN; PATHOPHYSIOLOGY; PRIORITY JOURNAL; PROTEIN DEFICIENCY; REVIEW; RODENT; STEM CELL; STOP CODON;

ADRENAL CORTEX HORMONES; ANIMALS; CYTOSKELETAL PROTEINS; DYSTROPHIN; HUMANS; MEMBRANE GLYCOPROTEINS; MUSCULAR DYSTROPHIES; SARCOGLYCANS;

EID: 0035450929     PISSN: 01656147     EISSN: None     Source Type: Journal    
DOI: 10.1016/S0165-6147(00)01770-3     Document Type: Review

References (58)

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14. Mdx mice inducibly expressing dystrophin provide insights into the potential of gene therapy for Duchenne muscular dystrophy
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39. + cells
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57. Expression of messenger RNA of the cardiac isoforms of troponin T and I in myopathic skeletal muscle