Directed alternative splicing in Nijmegen breakage syndrome: Proof of principle concerning its therapeutical application

Molecular Therapy

Volumn 24, Issue 1, 2016, Pages 117-124

  Salewsky, Bastian ^a   Hildebrand, Gabriele ^a   Rothe, Susanne ^a   Parplys, Ann Christin ^b   Radszewski, Janina ^a   Kieslich, Moritz ^a   Wessendorf, Petra ^a   Krenzlin, Harald ^a   Borgmann, Kerstin ^b   Nussenzweig, André ^c   Sperling, Karl ^a   Digweed, Martin ^a  

^a CHARITÉ UNIVERSITÄTSMEDIZIN BERLIN   (Germany)

^b UNIVERSITY MEDICAL CENTER HAMBURG EPPENDORF   (Germany)

^c NATIONAL CANCER INSTITUTE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ANTISENSE OLIGONUCLEOTIDE; MORPHOLINO OLIGONUCLEOTIDE; NIBRIN; PROTEIN P70; PROTEIN P80; PROTEIN P95; UNCLASSIFIED DRUG; CELL CYCLE PROTEIN; NBN PROTEIN, HUMAN; NUCLEAR PROTEIN;

ALTERNATIVE RNA SPLICING; ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; CONTROLLED STUDY; DNA REPLICATION; EXON; FIRING RATE; HUMAN; HUMAN CELL; IMMUNOPRECIPITATION; IN VITRO STUDY; IN VIVO STUDY; MOUSE; NIJMEGEN BREAKAGE SYNDROME; NONHUMAN; REVERSE TRANSCRIPTION POLYMERASE CHAIN REACTION; WESTERN BLOTTING; ANIMAL; ANTAGONISTS AND INHIBITORS; CELL LINE; CHILD; DISEASE MODEL; DRUG EFFECTS; FEMALE; GENE DELETION; GENETICS; MIDDLE AGED;

ALTERNATIVE SPLICING; ANIMALS; CELL CYCLE PROTEINS; CELL LINE; CHILD; DISEASE MODELS, ANIMAL; DNA REPLICATION; FEMALE; HUMANS; MICE; MIDDLE AGED; NIJMEGEN BREAKAGE SYNDROME; NUCLEAR PROTEINS; OLIGONUCLEOTIDES, ANTISENSE; SEQUENCE DELETION;

EID: 84957843148     PISSN: 15250016     EISSN: 15250024     Source Type: Journal    
DOI: 10.1038/mt.2015.144     Document Type: Article

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