Comparative Study of Liver Gene Transfer with AAV Vectors Based on Natural and Engineered AAV Capsids

Molecular Therapy

Volumn 23, Issue 12, 2015, Pages 1877-1887

  Wang, Lili ^a   Bell, Peter ^a   Somanathan, Suryanarayan ^a   Wang, Qiang ^a   He, Zhenning ^a   Yu, Hongwei ^a   McMenamin, Deirdre ^a   Goode, Tamara ^a   Calcedo, Roberto ^a   Wilson, James M ^a  

^a UNIVERSITY OF PENNSYLVANIA   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

PARVOVIRUS VECTOR; CAPSID PROTEIN;

ADENO ASSOCIATED VIRUS 2; ADENO ASSOCIATED VIRUS 8; ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL TISSUE; ARTICLE; COMPARATIVE STUDY; CONTROLLED STUDY; HEPATOCELLULAR CARCINOMA CELL LINE; HUMAN; HUMAN CELL; LIVER CELL; MALE; MOUSE; NONHUMAN; RHESUS MONKEY; TISSUE DISTRIBUTION; VIRAL GENE DELIVERY SYSTEM; VIRUS CAPSID; VIRUS RECOMBINANT; ANIMAL; C57BL MOUSE; CYTOLOGY; DEPENDOPARVOVIRUS; GENE THERAPY; GENE TRANSFER; GENE VECTOR; GENETIC ENGINEERING; GENETIC TRANSDUCTION; GENETICS; LIVER; METABOLISM;

ANIMALS; CAPSID PROTEINS; DEPENDOVIRUS; GENE TRANSFER TECHNIQUES; GENETIC ENGINEERING; GENETIC THERAPY; GENETIC VECTORS; HEPATOCYTES; HUMANS; LIVER; MACACA MULATTA; MALE; MICE; MICE, INBRED C57BL; TRANSDUCTION, GENETIC;

EID: 84952636705     PISSN: 15250016     EISSN: 15250024     Source Type: Journal    
DOI: 10.1038/mt.2015.179     Document Type: Article

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