Preclinical in vivo evaluation of pseudotyped adeno-associated virus vectors for liver gene therapy

Blood

Volumn 102, Issue 7, 2003, Pages 2412-2419

  Grimm, Dirk ^b   Zhou, Shangzhon ^b   Nakai, Hiroyuki ^b   Thomas, Clare E ^b   Storm, Theresa A ^b   Fuess, Sally ^b   Matsushita, Takashi ^b   Allen, James ^b   Surosky, Richard ^b   Lochrie, Michael ^b   Meuse, Leonard ^b   McClelland, Alan ^b   Colosi, Peter ^b   Kay, Mark A ^a  

^a STANFORD UNIVERSITY SCHOOL OF MEDICINE   (United States)

^b NONE

Author keywords

[No Author keywords available]

Indexed keywords

BLOOD CLOTTING FACTOR 9; DNA; NEUTRALIZING ANTIBODY; VIRUS VECTOR;

ADENO ASSOCIATED VIRUS; ANIMAL EXPERIMENT; ANIMAL TISSUE; ARTICLE; CONTROLLED STUDY; CROSS REACTION; DOSE RESPONSE; DRUG BLOOD LEVEL; EVALUATION; GENETIC TRANSDUCTION; HEMOPHILIA B; HUMAN; HUMAN CELL; IMMUNE RESPONSE; IMMUNOCOMPETENCE; IN VIVO STUDY; LIVER; LIVER DISEASE; MOUSE; NONHUMAN; PORTAL VEIN; PRIORITY JOURNAL; PROTEIN EXPRESSION; SEROTYPE; TAIL; TISSUE SPECIFICITY; VIRAL GENE THERAPY; VIRUS CAPSID; VIRUS GENOME; VIRUS NEUTRALIZATION; VIRUS PARTICLE; VIRUS PURIFICATION; VIRUS STRAIN;

EID: 0141482003     PISSN: 00064971     EISSN: None     Source Type: Journal    
DOI: 10.1182/blood-2003-02-0495     Document Type: Article

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