Sustained correction of bleeding disorder in hemophilia B mice by gene therapy

Proceedings of the National Academy of Sciences of the United States of America

Volumn 96, Issue 7, 1999, Pages 3906-3910

  Wang, Lili ^a   Takabe, Kazuaki ^a   Bidlingmaier, Scott M ^b   Ill, Charles R ^b   Verma, Inder M ^a  

^a SALK INSTITUTE FOR BIOLOGICAL STUDIES   (United States)

^b Orchestra Therapeutics Inc   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

BLOOD CLOTTING FACTOR 9; VIRUS VECTOR;

ADENO ASSOCIATED VIRUS; ANIMAL MODEL; ARTICLE; BLEEDING DISORDER; GENE EXPRESSION REGULATION; GENE TARGETING; GENE THERAPY; HEMOPHILIA B; IMMUNOBLOTTING; IMMUNOFLUORESCENCE TEST; LONG TERM CARE; MOUSE; NONHUMAN; PRIORITY JOURNAL; PROMOTER REGION; PROTEIN EXPRESSION; THROMBOPLASTIN TIME;

ANIMALS; CARCINOMA, HEPATOCELLULAR; DEPENDOVIRUS; DOGS; ENHANCER ELEMENTS (GENETICS); FACTOR IX; GENE THERAPY; GENETIC VECTORS; HEMOPHILIA B; HUMANS; LIVER; LIVER NEOPLASMS; MICE; MICE, INBRED C57BL; MICE, INBRED STRAINS; PROMOTER REGIONS (GENETICS); RECOMBINANT PROTEINS; TIME FACTORS; TRANSFECTION; TUMOR CELLS, CULTURED;

ADENO-ASSOCIATED VIRUS; ANIMALIA; RODENTIA;

EID: 0033616680     PISSN: 00278424     EISSN: None     Source Type: Journal    
DOI: 10.1073/pnas.96.7.3906     Document Type: Article

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