Pigtailed macaques as a model to study long-term safety of lentivirus vector-mediated gene therapy for hemoglobinopathies

Molecular Therapy Methods and Clinical Development

Volumn 1, Issue , 2014, Pages 14055-

  Kiem, Hans Peter ^a,b   Arumugam, Paritha I ^c   Burtner, Christopher R ^a   Fox, Catherine F ^c   Beard, Brian C ^a   Dexheimer, Phillip ^c   Adair, Jennifer E ^a,b   Malik, Punam ^c  

^a Fred Hutchinson Cancer Research Center   (United States)

^b UNIVERSITY OF WASHINGTON   (United States)

^c CINCINNATI CHILDREN'S HOSPITAL MEDICAL CENTER   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

HEMOGLOBIN F; HEMOGLOBIN GAMMA CHAIN; LENTIVIRUS VECTOR; TRANSCRIPTOME;

ARTICLE; AUTOPHAGY; CLONAL VARIATION; CONTROLLED STUDY; DRUG SAFETY; DRUG STABILITY; FOLLOW UP; GENE EXPRESSION; GENE INSERTION; GENETIC ASSOCIATION; GENOTOXICITY; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HEMOGLOBINOPATHY; LONG TERM CARE; MACACA NEMESTRINA; NONHUMAN; PRIORITY JOURNAL; VIRAL GENE THERAPY; WHOLE BODY RADIATION;

EID: 84942537325     PISSN: None     EISSN: 23290501     Source Type: Journal    
DOI: 10.1038/mtm.2014.55     Document Type: Article

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