Lymphoid regeneration from gene-corrected SCID-X1 subject-derived iPSCs

Cell Stem Cell

Volumn 16, Issue 4, 2015, Pages 367-372

  Menon, Tushar ^a   Firth, Amy L ^a   Scripture Adams, Deirdre D ^c   Galic, Zoran ^b,c   Qualls, Susan J ^a   Gilmore, William B ^a   Ke, Eugene ^a   Singer, Oded ^a   Anderson, Leif S ^a   Bornzin, Alexander R ^a   Alexander, Ian E ^d   Zack, Jerome A ^b,c   Verma, Inder M ^a  

^a SALK INSTITUTE FOR BIOLOGICAL STUDIES   (United States)

^b UNIVERSITY OF CALIFORNIA   (United States)

^c UNIVERSITY OF CALIFORNIA   (United States)

^d CHILDREN S HOSPITAL AT WESTMEAD   (Australia)

Author keywords

[No Author keywords available]

Indexed keywords

INTERLEUKIN 2 RECEPTOR GAMMA; TRANSCRIPTION ACTIVATOR LIKE EFFECTOR NUCLEASE; BACTERIAL PROTEIN; DNA LIGASE; LEUKOCYTE ANTIGEN;

ARTICLE; CASE REPORT; CELL DIFFERENTIATION; CELL LINEAGE; CELL MATURATION; CELL REGENERATION; CONTROLLED STUDY; EMBRYO; GENE EXPRESSION; HEMATOPOIETIC STEM CELL; HUMAN; HUMAN CELL; INFANT; MULTIPOTENT STEM CELL; MYELOID PROGENITOR CELL; NATURAL KILLER CELL; PLURIPOTENT STEM CELL; PRE T LYMPHOCYTE; PRIORITY JOURNAL; RNA EDITING; RNA SPLICING; SPLICING DEFECT; WILD TYPE; X LINKED SEVERE COMBINED IMMUNODEFICIENCY; ADOPTIVE IMMUNOTHERAPY; CELL LINE; DNA REPAIR; GENE THERAPY; GENETICS; INDUCED PLURIPOTENT STEM CELL; METABOLISM; MUTATION; PHYSIOLOGY; PROCEDURES; REGENERATION; REGENERATIVE MEDICINE; TRANSPLANTATION; X-LINKED COMBINED IMMUNODEFICIENCY DISEASES;

ANTIGENS, CD; BACTERIAL PROTEINS; CELL DIFFERENTIATION; CELL LINE; DNA REPAIR; DNA REPAIR ENZYMES; GENETIC THERAPY; HUMANS; IMMUNOTHERAPY, ADOPTIVE; INDUCED PLURIPOTENT STEM CELLS; INFANT; INTERLEUKIN RECEPTOR COMMON GAMMA SUBUNIT; KILLER CELLS, NATURAL; MUTATION; PRECURSOR CELLS, T-LYMPHOID; REGENERATION; REGENERATIVE MEDICINE; X-LINKED COMBINED IMMUNODEFICIENCY DISEASES;

EID: 84926200105     PISSN: 19345909     EISSN: 18759777     Source Type: Journal    
DOI: 10.1016/j.stem.2015.02.005     Document Type: Article

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