Gene therapy that works

Science

Volumn 341, Issue 6148, 2013, Pages 853-855

  Verma, Inder M ^a  

^a SALK INSTITUTE FOR BIOLOGICAL STUDIES   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

BRAIN; CHILD HEALTH; DISEASE TREATMENT; GENE; GENETIC ANALYSIS; GENOTOXICITY; IMMUNE RESPONSE; NEUROLOGY;

BONE MARROW TRANSPLANTATION; CELL GROWTH; CELL PROLIFERATION; CELL THERAPY; GENE EXPRESSION; GENE MUTATION; GENE THERAPY; GENETIC DISORDER; HEMATOPOIETIC STEM CELL; HOST CELL; HUMAN; IMMUNE DEFICIENCY; PRIORITY JOURNAL; SHORT SURVEY; GENETICS; HEMATOPOIETIC STEM CELL TRANSPLANTATION; MALE; METABOLISM; METACHROMATIC LEUKODYSTROPHY; METHODOLOGY; NOTE; WISKOTT ALDRICH SYNDROME;

CEREBROSIDE SULFATASE; WISKOTT ALDRICH SYNDROME PROTEIN;

CEREBROSIDE-SULFATASE; GENETIC THERAPY; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HEMATOPOIETIC STEM CELLS; HUMANS; LEUKODYSTROPHY, METACHROMATIC; MALE; WISKOTT-ALDRICH SYNDROME; WISKOTT-ALDRICH SYNDROME PROTEIN;

EID: 84882776567     PISSN: 00368075     EISSN: 10959203     Source Type: Journal    
DOI: 10.1126/science.1242551     Document Type: Short Survey

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