Variable correction of Artemis deficiency by I-Sce1-Meganuclease-assisted homologous recombination in murine hematopoietic stem cells

Gene Therapy

Volumn 21, Issue 5, 2014, Pages 529-532

  Riviere J ^a,b   Hauer, J ^a,c   Poirot, L ^d   Brochet, J ^a,b   Souque, P ^e   Mollier, K ^e   Gouble, A ^d   Charneau, P ^e   Fischer, A ^a,b   Paques F ^d   De Villartay, J P ^a,b   Cavazzana, M ^a,b,f  

^a HÔPITAL NECKER ENFANTS MALADES   (France)

^b IMAGINE INSTITUTE   (France)

^c UNIVERSITY HOSPITAL DÜSSELDORF   (Germany)

^d Arvid Wallgrens Backe 20   (France)

^e INSTITUT PASTEUR   (France)

^f ASSISTANCE PUBLIQUE HÔPITAUX DE PARIS   (France)

Author keywords

[No Author keywords available]

Indexed keywords

ENDONUCLEASE; I SCE1 MEGANUCLEASE; LENTIVIRUS VECTOR; SELF INACTIVATING INTEGRASE DEFECTIVE LENTIVIRAL VECTOR ARTEMIS GENE; SELF INACTIVATING INTEGRASE DEFECTIVE LENTIVIRAL VECTOR CYTOMEGALOVIRUS I SCE1 MEGANUCLEASE; UNCLASSIFIED DRUG; DCLRE1C PROTEIN, MOUSE; NUCLEAR PROTEIN; SACCHAROMYCES CEREVISIAE PROTEIN; SCEI PROTEIN, S CEREVISIAE; TYPE II SITE SPECIFIC DEOXYRIBONUCLEASE;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ARTEMIS GENE; ARTICLE; DNA TEMPLATE; DOUBLE STRANDED DNA BREAK; GENE; GENE EXPRESSION REGULATION; GENE MUTATION; GENE TARGETING; GENETIC ENGINEERING; GENETIC TRANSDUCTION; HEMATOPOIETIC STEM CELL; HOMOLOGOUS RECOMBINATION; KNOCKOUT MOUSE; LYMPHOCYTE DIFFERENTIATION; MOUSE; NONHUMAN; PRIORITY JOURNAL; ANIMAL; CYTOLOGY; DEFICIENCY; DNA REPAIR; GENE THERAPY; GENE VECTOR; GENETICS; LENTIVIRINAE; MUTATION; PROCEDURES;

ANIMALS; DEOXYRIBONUCLEASES, TYPE II SITE-SPECIFIC; DNA BREAKS, DOUBLE-STRANDED; DNA REPAIR; ENDONUCLEASES; GENETIC THERAPY; GENETIC VECTORS; HEMATOPOIETIC STEM CELLS; HOMOLOGOUS RECOMBINATION; LENTIVIRUS; MICE; MICE, KNOCKOUT; MUTATION; NUCLEAR PROTEINS; SACCHAROMYCES CEREVISIAE PROTEINS; TRANSDUCTION, GENETIC;

EID: 84900012210     PISSN: 09697128     EISSN: 14765462     Source Type: Journal    
DOI: 10.1038/gt.2014.20     Document Type: Article

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