Transcription activator-like effector nuclease (TALEN)-mediated Gene correction in integration-free β-Thalassemia induced pluripotent stem cells

Journal of Biological Chemistry

Volumn 288, Issue 48, 2013, Pages 34671-34679

  Ma, Ning ^a   Liao, Baojian ^a   Zhang, Hui ^a   Wang, Linli ^a   Shan, Yongli ^a   Xue, Yanting ^a,b   Huang, Ke ^a   Chen, Shubin ^a   Zhou, Xiaoxiao ^a   Chen, Yang ^a   Pei, Duanqing ^a   Pan, Guangjin ^a  

^a GUANGZHOU INSTITUTES OF BIOMEDICINE AND HEALTH   (China)

^b UNIVERSITY OF SCIENCE AND TECHNOLOGY OF CHINA   (China)

Author keywords

[No Author keywords available]

Indexed keywords

CORRECTION PROCESS; DISEASE MODELING; GENE CORRECTION; HEMATOPOIETIC PROGENITOR CELLS; HOMOLOGOUS RECOMBINATION; INDUCED PLURIPOTENT STEM CELLS; PATIENT SPECIFIC; THERAPEUTIC SOLUTIONS;

CELL CULTURE; GENES; HEMOGLOBIN; INTEGRATION; STEM CELLS;

TRANSCRIPTION;

HEMOGLOBIN BETA CHAIN; NUCLEASE; TRANSCRIPTION ACTIVATOR LIKE EFFECTOR NUCLEASE; UNCLASSIFIED DRUG;

ARTICLE; BETA THALASSEMIA; CELL DIFFERENTIATION; CONTROLLED STUDY; ENZYME ACTIVITY; ERYTHROBLAST; GENE; GENE CORRECTION; GENE MUTATION; GENETIC PROCEDURES; HBB GENE; HUMAN; HUMAN CELL; PLURIPOTENT STEM CELL; PRIORITY JOURNAL; PROTEIN EXPRESSION;

EID: 84889000317     PISSN: 00219258     EISSN: 1083351X     Source Type: Journal    
DOI: 10.1074/jbc.M113.496174     Document Type: Article

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