Reversal of aberrant splicing of β-thalassaemia allele (IVS-2-654 C→T) by antisense RNA expression vector in cultured human erythroid cells

British Journal of Haematology

Volumn 111, Issue 1, 2000, Pages 351-358

  Gong, Lan ^a   Gu, Xiao Feng ^a   Chen, Yun Di ^a   Ren, Zhao Rui ^a   Huang, Shu Zhen ^a   Zeng, Yi Tao ^a  

^a SHANGHAI CHILDREN S HOSPITAL   (China)

Author keywords

thalassaemia; Antisense RNA; Erythroid cell; Gene therapy; Splicing defect

Indexed keywords

BETA GLOBIN; COMPLEMENTARY RNA;

ADULT; ARTICLE; BETA THALASSEMIA; CHILD; CLINICAL ARTICLE; ERYTHROID CELL; EXPRESSION VECTOR; FEMALE; GENE THERAPY; HUMAN; HUMAN CELL; MALE; PRIORITY JOURNAL; REVERSE TRANSCRIPTION POLYMERASE CHAIN REACTION; RNA SPLICING;

ADULT; BETA-THALASSEMIA; CELLS, CULTURED; CHILD; CHILD, PRESCHOOL; ERYTHROID PROGENITOR CELLS; FEMALE; GENE THERAPY; HUMANS; MALE; MIDDLE AGED; RNA SPLICING; RNA, ANTISENSE; TRANSFECTION;

EID: 0033765803     PISSN: 00071048     EISSN: None     Source Type: Journal    
DOI: 10.1046/j.1365-2141.2000.02311.x     Document Type: Article

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