Haematopoietic stem cell transplantation for SCID patients: Where do we stand?

British Journal of Haematology

Volumn 160, Issue 2, 2013, Pages 146-152

  Cavazzana Calvo, Marina ^a,b,c,d   André Schmutz, Isabelle ^b,c,d   Fischer, Alain ^a,b,c  

^a HÔPITAL NECKER ENFANTS MALADES   (France)

^b INSERM   (France)

^c IMAGINE INSTITUTE   (France)

^d ASSISTANCE PUBLIQUE HÔPITAUX DE PARIS   (France)

Author keywords

Gene therapy; Haematopoietic stem cell transplantation; Immunological reconstitution; Severe combined immunodeficiency; Umbilical cord blood transplantation

Indexed keywords

RETROVIRUS VECTOR;

ADENOSINE DEAMINASE DEFICIENCY; ADOPTIVE TRANSFER; ALLOGENEIC HEMATOPOIETIC STEM CELL TRANSPLANTATION; CORD BLOOD STEM CELL TRANSPLANTATION; GENE THERAPY; GRAFT VERSUS HOST REACTION; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HLA MATCHING; HUMAN; LONG TERM SURVIVAL; MOLECULAR DIAGNOSIS; NATURAL KILLER CELL; NEWBORN SCREENING; NONHUMAN; OVERALL SURVIVAL; PRIORITY JOURNAL; REVIEW; SEVERE COMBINED IMMUNODEFICIENCY; SIBLING; SURVIVAL RATE; UNRELATED DONORS;

CORD BLOOD STEM CELL TRANSPLANTATION; CYTOKINES; EUROPE; GENETIC THERAPY; GRAFT REJECTION; GRAFT VS HOST DISEASE; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HISTOCOMPATIBILITY; HUMANS; INFANT; INFANT, NEWBORN; LYMPHOCYTE SUBSETS; LYMPHOCYTE TRANSFUSION; LYMPHOPOIESIS; NEONATAL SCREENING; SEVERE COMBINED IMMUNODEFICIENCY; THYMUS GLAND; TISSUE DONORS; TRANSPLANTATION, HOMOLOGOUS; TREATMENT OUTCOME; UNITED STATES;

EID: 84872271463     PISSN: 00071048     EISSN: 13652141     Source Type: Journal    
DOI: 10.1111/bjh.12119     Document Type: Review

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