Neonatal diagnosis of severe combined immunodeficiency leads to significantly improved survival outcome: The case for newborn screening

Blood

Volumn 117, Issue 11, 2011, Pages 3243-3246

  Brown, Lucinda ^a   Xu Bayford, Jinhua ^a   Allwood, Zoe ^a   Slatter, Mary ^b   Cant, Andrew ^b   Davies, E Graham ^a   Veys, Paul ^a   Gennery, Andrew R ^b   Gaspar, H Bobby ^a,c  

^a GREAT ORMOND STREET HOSPITAL   (United Kingdom)

^b NEWCASTLE GENERAL HOSPITAL   (United Kingdom)

^c UNIVERSITY COLLEGE LONDON   (United Kingdom)

Author keywords

[No Author keywords available]

Indexed keywords

ARTICLE; DONOR SELECTION; FAMILY HISTORY; GENETIC ANALYSIS; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMAN; INFECTION RATE; MAJOR CLINICAL STUDY; NEWBORN; NEWBORN SCREENING; PRIORITY JOURNAL; SEVERE COMBINED IMMUNODEFICIENCY; SURVIVAL RATE; TREATMENT OUTCOME; UNITED KINGDOM;

EID: 79953082197     PISSN: 00064971     EISSN: 15280020     Source Type: Journal    
DOI: 10.1182/blood-2010-08-300384     Document Type: Article

References (13)

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