Clinical practice :NTBC therapy for tyrosinemia type 1: How much is enough?

European Journal of Pediatrics

Volumn 169, Issue 6, 2010, Pages 689-693

  El Karaksy, Hanaa ^a   Rashed, Mohmmad ^c   El Sayed, Rokaya ^a   El Raziky, Mona ^a   El Koofy, Nehal ^a   El Hawary, Manal ^b   Al Dirbashi, Osama ^c  

^a CAIRO UNIVERSITY   (Egypt)

^b Fayoum University   (Egypt)

^c KING FAISAL SPECIALIST HOSPITAL AND RESEARCH CENTER   (Saudi Arabia)

Author keywords

Children; NTBC; Tyrosinemia

Indexed keywords

ALKALINE PHOSPHATASE; ALPHA FETOPROTEIN; CALCIUM; NITISINONE; PHOSPHATE; SUCCINYLACETONE; CYCLOHEXANONE DERIVATIVE; ENZYME INHIBITOR; HEPTANOIC ACID DERIVATIVE; NITROBENZOIC ACID DERIVATIVE;

ALKALINE PHOSPHATASE BLOOD LEVEL; ALPHA FETOPROTEIN BLOOD LEVEL; ARTICLE; BLOOD LEVEL; CALCIUM BLOOD LEVEL; CASE REPORT; CHILD; DRUG DOSE INCREASE; EGYPT; FEMALE; HUMAN; INFANT; LIVER FUNCTION; PHOSPHATE BLOOD LEVEL; PRESCHOOL CHILD; PRIORITY JOURNAL; RECOMMENDED DRUG DOSE; RICKETS; SUCCINYLACETONE BLOOD LEVEL; TYROSINEMIA; BLOOD; COST BENEFIT ANALYSIS; DOSE RESPONSE; DRUG COST; ECONOMICS;

CHILD, PRESCHOOL; COST-BENEFIT ANALYSIS; CYCLOHEXANONES; DOSE-RESPONSE RELATIONSHIP, DRUG; DRUG COSTS; EGYPT; ENZYME INHIBITORS; FEMALE; HEPTANOATES; HUMANS; INFANT; NITROBENZOATES; TYROSINEMIAS;

EID: 77952090968     PISSN: 03406199     EISSN: None     Source Type: Journal    
DOI: 10.1007/s00431-009-1090-1     Document Type: Article

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