In vivo gene transfer strategies to achieve partial correction of von willebrand disease

Human Gene Therapy

Volumn 23, Issue 6, 2012, Pages 576-588

  Wang, Lan ^a,b   Rosenberg, Jonathan B ^a   De, Bishnu P ^a   Ferris, Barbara ^a   Wang, Rui ^a   Rivella, Stefano ^a   Kaminsky, Stephen M ^a   Crystal, Ronald G ^a  

^a WEILL CORNELL MEDICAL COLLEGE   (United States)

^b SICHUAN UNIVERSITY   (China)

Author keywords

[No Author keywords available]

Indexed keywords

ADENOVIRUS VECTOR; COMPLEMENTARY DNA; LENTIVIRUS VECTOR; POLYMER; VON WILLEBRAND FACTOR;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; BLEEDING; BLEEDING TIME; CONTROLLED STUDY; GENE EXPRESSION; IN VITRO STUDY; IN VIVO GENE TRANSFER; IN VIVO STUDY; LIVER; MOUSE; NEWBORN; NONHUMAN; NUCLEOTIDE SEQUENCE; TRANS SPLICING; VIRAL GENE DELIVERY SYSTEM; VON WILLEBRAND DISEASE;

ANIMALS; DEPENDOVIRUS; GENETIC THERAPY; GENETIC VECTORS; IMMUNOHISTOCHEMISTRY; LIVER; MICE; MICE, KNOCKOUT; VON WILLEBRAND DISEASES;

ADENO-ASSOCIATED VIRUS; LENTIVIRUS; MURINAE; MUS;

EID: 84864331568     PISSN: 10430342     EISSN: 15577422     Source Type: Journal    
DOI: 10.1089/hum.2011.238     Document Type: Article

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