Functional cystic fibrosis transmembrane conductance regulator expression in cystic fibrosis airway epithelial cells by AAV6.2-mediated segmental trans-splicing

Human Gene Therapy

Volumn 20, Issue 3, 2009, Pages 267-281

  Song, Yuhu ^a   Lou, Howard H ^a   Boyer, Julie L ^a   Limberis, Maria P ^b   Vandenberghe, Luk H ^b   Hackett, Neil R ^a   Leopold, Philip L ^a   Wilson, James M ^b   Crystal, Ronald G ^a  

^a WEILL CORNELL MEDICAL COLLEGE   (United States)

^b UNIVERSITY OF PENNSYLVANIA   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

CHLORIDE; COMPLEMENTARY DNA; CYCLIC AMP; MESSENGER RNA; PARVOVIRUS VECTOR; TRANSMEMBRANE CONDUCTANCE REGULATOR;

ARTICLE; CHLORIDE CONDUCTANCE; CONTROLLED STUDY; CYSTIC FIBROSIS; GENE CONSTRUCT; GENETIC ENGINEERING; GENETIC TRANSFECTION; HUMAN; HUMAN CELL; MICROINJECTION; PLASMID; PROMOTER REGION; PROTEIN EXPRESSION; PROTEIN FUNCTION; RESPIRATORY EPITHELIUM; SEROTYPE; TARGET CELL; TRANS SPLICING; VIRAL GENE DELIVERY SYSTEM;

ADENOVIRIDAE; ANIMALS; CELL LINE; CYSTIC FIBROSIS; CYSTIC FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR; EPITHELIAL CELLS; GENETIC VECTORS; HUMANS; RATS; RNA PRECURSORS; RNA, MESSENGER; TRANS-SPLICING;

EID: 62549141507     PISSN: 10430342     EISSN: None     Source Type: Journal    
DOI: 10.1089/hum.2008.173     Document Type: Article

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