Systemic trans-splicing adeno-associated viral delivery efficiently transduces the heart of adult mdx mouse, a model for duchenne muscular dystrophy

Human Gene Therapy

Volumn 20, Issue 11, 2009, Pages 1319-1328

  Ghosh, Arkasubhra ^a   Yue, Yongping ^a   Shin, Jin Hong ^a   Duan, Dongsheng ^a  

^a University of Missouri   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ALKALINE PHOSPHATASE; MYOSIN HEAVY CHAIN BETA; PARVOVIRUS VECTOR;

ADENO ASSOCIATED VIRUS; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CD4+ T LYMPHOCYTE; CD8+ T LYMPHOCYTE; CONTROLLED STUDY; EMBRYO; EXPERIMENTAL MODEL; EXPERIMENTAL MOUSE; FEMALE; GENETIC TRANSDUCTION; HEART MUSCLE; INFLAMMATION; MACROPHAGE; MDX MICE; MOUSE; MOUSE STRAIN; NEWBORN; NONHUMAN; PROTEIN EXPRESSION; SKELETAL MUSCLE; TRANS SPLICING; VIRAL GENE DELIVERY SYSTEM; X CHROMOSOME LINKED MUSCULAR DYSTROPHIC MOUSE; ANALYSIS OF VARIANCE; ANIMAL; CARDIOMYOPATHIES; COMPLICATION; DEPENDOPARVOVIRUS; DUCHENNE MUSCULAR DYSTROPHY; FLUORESCENT ANTIBODY TECHNIQUE; GENE THERAPY; GENE VECTOR; GENETICS; HEART; IMMUNOHISTOCHEMISTRY; PROCEDURES;

ALKALINE PHOSPHATASE; ANALYSIS OF VARIANCE; ANIMALS; CARDIOMYOPATHIES; DEPENDOVIRUS; FLUORESCENT ANTIBODY TECHNIQUE; GENE THERAPY; GENETIC VECTORS; HEART; IMMUNOHISTOCHEMISTRY; MICE; MICE, INBRED MDX; MUSCULAR DYSTROPHY, DUCHENNE; TRANS-SPLICING; TRANSDUCTION, GENETIC; GENETIC THERAPY;

MUS;

EID: 70449119011     PISSN: 10430342     EISSN: None     Source Type: Journal    
DOI: 10.1089/hum.2009.058     Document Type: Article

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