-
1
-
-
0038685648
-
Gene therapy progress and prospects: Gene therapy for the hemophilias
-
Walsh CE. Gene therapy progress and prospects: gene therapy for the hemophilias. Gene Ther 2003; 10: 999-1003.
-
(2003)
Gene Ther
, vol.10
, pp. 999-1003
-
-
Walsh, C.E.1
-
3
-
-
0032821708
-
Prospects for in utero human gene therapy
-
Zanjani ED, Anderson WF. Prospects for in utero human gene therapy. Science 1999; 285: 2084-8.
-
(1999)
Science
, vol.285
, pp. 2084-2088
-
-
Zanjani, E.D.1
Anderson, W.F.2
-
4
-
-
0032796974
-
Perspective: Fetal gene therapy
-
Walsh CE. Perspective: fetal gene therapy. Gene Ther 1999; 6: 1200-1.
-
(1999)
Gene Ther
, vol.6
, pp. 1200-1201
-
-
Walsh, C.E.1
-
5
-
-
0033121139
-
Prenatal gene therapy: Can the technical hurdles be overcome?
-
Senut MC, Gage FH. Prenatal gene therapy: can the technical hurdles be overcome? Mol Med Today 1999; 5: 152-6.
-
(1999)
Mol Med Today
, vol.5
, pp. 152-156
-
-
Senut, M.C.1
Gage, F.H.2
-
6
-
-
0029996147
-
In vivo gene delivery and stable transduction of nondividing cells by a lentiviral vector
-
Naldini L, Blomer U, Gallay P, Ory D, Mulligan R, Gage F H, et al. In vivo gene delivery and stable transduction of nondividing cells by a lentiviral vector. Science 1996; 272: 263-7.
-
(1996)
Science
, vol.272
, pp. 263-267
-
-
Naldini, L.1
Blomer, U.2
Gallay, P.3
Ory, D.4
Mulligan, R.5
Gage, F.H.6
-
7
-
-
0034254320
-
Theraputic levels of human factor VIII and IX using HIV-1-based lentiviral vectors in mouse liver
-
Park F, Ohashi K, Kay MA. Theraputic levels of human factor VIII and IX using HIV-1-based lentiviral vectors in mouse liver. Blood 2000; 96: 1173-6.
-
(2000)
Blood
, vol.96
, pp. 1173-1176
-
-
Park, F.1
Ohashi, K.2
Kay, M.A.3
-
8
-
-
0034180682
-
The application of a lentiviral vector for gene transfer in fetal human hepatocytes
-
Zahler MH, Irani A, Malhi H, Reutens AT, Albanese C, Bouzahzah B, et al. The application of a lentiviral vector for gene transfer in fetal human hepatocytes. J Gene Med 2000; 2: 186-93.
-
(2000)
J Gene Med
, vol.2
, pp. 186-193
-
-
Zahler, M.H.1
Irani, A.2
Malhi, H.3
Reutens, A.T.4
Albanese, C.5
Bouzahzah, B.6
-
9
-
-
0346035738
-
Efficient transduction of liver and muscle after in utero injection of lentiviral vectors with different pseudotypes
-
MacKenzie TC, Kobinger GP, Kootstra NA, Radu A, Sena-Esteves M, Bouchard S, et al. Efficient transduction of liver and muscle after in utero injection of lentiviral vectors with different pseudotypes. Mol Ther 2002; 6: 349-58.
-
(2002)
Mol Ther
, vol.6
, pp. 349-358
-
-
MacKenzie, T.C.1
Kobinger, G.P.2
Kootstra, N.A.3
Radu, A.4
Sena-Esteves, M.5
Bouchard, S.6
-
10
-
-
2942584240
-
Expression of human clotting factor mediated by recombinant lentiviral vector in cultured cells and hemophilia B mice
-
Zhu HZ, Chen XG, Li F, Gong JL, Xue JL. Expression of human clotting factor mediated by recombinant lentiviral vector in cultured cells and hemophilia B mice. Chin Sci Bull 2003; 48: 2196-200.
-
(2003)
Chin Sci Bull
, vol.48
, pp. 2196-2200
-
-
Zhu, H.Z.1
Chen, X.G.2
Li, F.3
Gong, J.L.4
Xue, J.L.5
-
11
-
-
0036468677
-
Germline transmission and tissue-specific expression of transgenes delivered by lentiviral vectors
-
Lois C, Hong EJ, Pease S, Brown EJ, Baltimore D. Germline transmission and tissue-specific expression of transgenes delivered by lentiviral vectors. Science 2002; 295: 868-72.
-
(2002)
Science
, vol.295
, pp. 868-872
-
-
Lois, C.1
Hong, E.J.2
Pease, S.3
Brown, E.J.4
Baltimore, D.5
-
12
-
-
0036371236
-
Sustained delivery of therapeutic concentrations of human clotting factor IX - A comparison of adenoviral and AAV vectors administered in utero
-
Schneider H, Muhle C, Douar AM, Waddington S, Jiang QJ, Mark KD. Sustained delivery of therapeutic concentrations of human clotting factor IX - a comparison of adenoviral and AAV vectors administered in utero. J Gene Med 2002; 4: 46-53.
-
(2002)
J Gene Med
, vol.4
, pp. 46-53
-
-
Schneider, H.1
Muhle, C.2
Douar, A.M.3
Waddington, S.4
Jiang, Q.J.5
Mark, K.D.6
-
13
-
-
0036137639
-
Production of human clotting factor IX without toxicity in mice after vascular delivery of alentiviral vector
-
Tsui LV, Kelly M, Zayek N, Rojas V, Ho K, Ge Y, et al. Production of human clotting factor IX without toxicity in mice after vascular delivery of alentiviral vector. Nat Biotechnol 2002; 20: 53-7.
-
(2002)
Nat Biotechnol
, vol.20
, pp. 53-57
-
-
Tsui, L.V.1
Kelly, M.2
Zayek, N.3
Rojas, V.4
Ho, K.5
Ge, Y.6
-
14
-
-
0001961415
-
Experiences with recombinant factor VIII products: Development of inhibitors and immune tolerance therapy
-
Scharrer I, Neutzling O, Schwaab R, Oldenburg J, Ehrlich H. Experiences with recombinant factor VIII products: development of inhibitors and immune tolerance therapy. Ann Hematol 1998; 76: A1-6.
-
(1998)
Ann Hematol
, vol.76
-
-
Scharrer, I.1
Neutzling, O.2
Schwaab, R.3
Oldenburg, J.4
Ehrlich, H.5
|