An exon-specific U1 small nuclear RNA (snRNA) strategy to correct splicing defects

Human Molecular Genetics

Volumn 21, Issue 11, 2012, Pages 2389-2398

  Alanis, Eugenio Fernandez ^a   Pinotti, Mirko ^b   Mas, Andrea Dal ^a   Balestra, Dario ^b   Cavallari, Nicola ^b   Rogalska, Malgorzata E ^a   Bernardi, Francesco ^b   Pagani, Franco ^a  

^a INTERNATIONAL CENTRE FOR GENETIC ENGINEERING AND BIOTECHNOLOGY   (Italy)

^b UNIVERSITY OF FERRARA   (Italy)

Author keywords

[No Author keywords available]

Indexed keywords

BLOOD CLOTTING FACTOR 9; COMPLEMENTARY DNA; POLYPYRIMIDINE TRACT BINDING PROTEIN; SMALL NUCLEAR RNA; SURVIVAL MOTOR NEURON PROTEIN 2; TRANSMEMBRANE CONDUCTANCE REGULATOR;

ARTICLE; CHROMOSOME; CONTROLLED STUDY; CYSTIC FIBROSIS; DOWNSTREAM PROCESSING; EXON; GENE CONSTRUCT; GENE EXPRESSION; GENE MUTATION; GENETIC VARIABILITY; HEMOPHILIA B; HUMAN; HUMAN CELL; IN VIVO STUDY; INTRON; NONHUMAN; PRIORITY JOURNAL; RNA SPLICING; SPINAL MUSCULAR ATROPHY; SPLICING DEFECT;

ALTERNATIVE SPLICING; CYSTIC FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR; EXONS; HEMOPHILIA B; HUMANS; INTRONS; MUSCULAR ATROPHY, SPINAL; MUTATION; RNA PRECURSORS; RNA SPLICE SITES; RNA SPLICING; RNA, SMALL NUCLEAR;

EID: 84861134371     PISSN: 09646906     EISSN: 14602083     Source Type: Journal    
DOI: 10.1093/hmg/dds045     Document Type: Article

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