Comparative analysis of FV vectors with human α- or β-globin gene regulatory elements for the correction of β-thalassemia

Gene Therapy

Volumn 19, Issue 3, 2012, Pages 303-311

  Morianos, I ^a   Siapati, E K ^a   Pongas, G ^a   Vassilopoulos, G ^a,b  

^a BIOMEDICAL RESEARCH FOUNDATION   (Greece)

^b UNIVERSITY OF THESSALY   (Greece)

Author keywords

globin; foamy virus; HS40; thalassemia

Indexed keywords

ALPHA GLOBIN; BETA GLOBIN; CD71 ANTIGEN; LIPOCORTIN 5; VIRUS VECTOR;

ANIMAL CELL; ANIMAL TISSUE; APOPTOSIS; ARTICLE; BETA THALASSEMIA; CD34 SELECTION; COMPARATIVE STUDY; CONTROLLED STUDY; ERYTHROPOIESIS; EX VIVO STUDY; GENE CONTROL; GENE EXPRESSION; GENE LOCUS; HEMATOPOIETIC STEM CELL; HUMAN; HUMAN CELL; MOUSE; NONHUMAN; PHENOTYPE; PRIORITY JOURNAL; REGULATOR GENE; SPUMA VIRUS; TRANSGENE;

ALPHA-GLOBINS; ANIMALS; BETA-GLOBINS; BETA-THALASSEMIA; CELL LINE; DISEASE MODELS, ANIMAL; FEMALE; GENE EXPRESSION; GENE ORDER; GENE THERAPY; GENETIC VECTORS; HEMATOPOIETIC STEM CELLS; HUMANS; LOCUS CONTROL REGION; MICE; MICE, INBRED C57BL; MICE, TRANSGENIC; SPUMAVIRUS; TRANSDUCTION, GENETIC;

HUMAN SPUMARETROVIRUS; MURINAE;

EID: 84858006799     PISSN: 09697128     EISSN: 14765462     Source Type: Journal    
DOI: 10.1038/gt.2011.98     Document Type: Article

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