Development of viral vectors for gene therapy of β-chain hemoglobinopathies: Optimization of a γ-globin gene expression cassette

Blood

Volumn 93, Issue 7, 1999, Pages 2208-2216

  Li, Qiliang ^a   Emery, David W ^a   Fernandez, Magali ^a   Han, Hemei ^a   Stamatoyannopoulos, George ^a  

^a UNIVERSITY OF WASHINGTON SCHOOL OF MEDICINE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

IMMUNOGLOBULIN; VIRUS VECTOR;

ARTICLE; ENHANCER REGION; GENE DELETION; GENE TARGETING; GENE THERAPY; HEMOGLOBINOPATHY; HUMAN; INTRON; MOLECULAR CLONING; NONHUMAN; PRIORITY JOURNAL; PROMOTER REGION; RETROVIRUS;

EID: 0033121071     PISSN: 00064971     EISSN: None     Source Type: Journal    
DOI: 10.1182/blood.v93.7.2208     Document Type: Article

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