Gene delivery of wild-type rhodopsin rescues retinal function in an autosomal dominant retinitis pigmentosa mouse model

Advances in Experimental Medicine and Biology

Volumn 723, Issue , 2012, Pages 199-205

  Mao, Haoyu ^a   Gorbatyuk, Marina S ^b   Hauswirth, William W ^a,c   Lewin, Alfred S ^a  

^a UNIVERSITY OF FLORIDA   (United States)

^b UNIVERSITY OF NORTH TEXAS HEALTH SCIENCE CENTER   (United States)

^c UNIVERSITY OF FLORIDA COLLEGE OF MEDICINE   (United States)

Author keywords

Autosomal Dominant Retinitis Pigmentosa; Gene Delivery; Rhodopsin

Indexed keywords

ADENOVIRUS VECTOR; HISTIDINE; PROLINE; SMALL INTERFERING RNA;

AMINO ACID SUBSTITUTION; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; AUTOSOMAL DOMINANT RETINITIS PIGMENTOSA; CONFERENCE PAPER; ELECTRORETINOGRAM; GENE; MOUSE; NONHUMAN; NUCLEOTIDE SEQUENCE; PHOTORECEPTOR; PRIORITY JOURNAL; RETINA DEGENERATION; RETINITIS PIGMENTOSA; RHO301 GENE; TRANSGENIC MOUSE; VIRAL GENE DELIVERY SYSTEM;

ANIMALS; DEPENDOVIRUS; DISEASE MODELS, ANIMAL; ELECTRORETINOGRAPHY; GENE THERAPY; GENE TRANSFER TECHNIQUES; GENES, DOMINANT; INTERMEDIATE FILAMENT PROTEINS; MEMBRANE GLYCOPROTEINS; MICE; NERVE TISSUE PROTEINS; PHOTORECEPTOR CELLS, VERTEBRATE; RETINITIS PIGMENTOSA; RHODOPSIN;

ADENO-ASSOCIATED VIRUS; ANIMALIA; MUS; MUS MUSCULUS;

EID: 84855978522     PISSN: 00652598     EISSN: None     Source Type: Book Series    
DOI: 10.1007/978-1-4614-0631-0_27     Document Type: Conference Paper

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