Gene therapy for haemophilia: A long and winding road

Journal of Thrombosis and Haemostasis

Volumn 9, Issue 1 S, 2011, Pages 2-11

  High, K A ^a  

^a UNIVERSITY OF PENNSYLVANIA   (United States)

Author keywords

AAV; Factor VIIa; Gene therapy; Haemophilia A; Haemophilia B; Inhibitors

Indexed keywords

BLOOD CLOTTING FACTOR 7A; CYCLOSPORIN; GAMMA INTERFERON; LENTIVIRUS VECTOR; LIPOPROTEIN; MYCOPHENOLIC ACID 2 MORPHOLINOETHYL ESTER; RAPAMYCIN;

ADRENOLEUKODYSTROPHY; GENE THERAPY; GENETIC DISORDER; HEMOPHILIA; HEMOPHILIA A; HEMOPHILIA B; HUMAN; HUMAN GENOME; LIVER CELL; LIVER DISEASE; NONHUMAN; PRIORITY JOURNAL; REVIEW;

ANIMALS; GENE THERAPY; GENETIC VECTORS; HEMOPHILIA A; HUMANS;

EID: 79960649903     PISSN: 15387933     EISSN: 15387836     Source Type: Journal    
DOI: 10.1111/j.1538-7836.2011.04369.x     Document Type: Review

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