Long-term expression of human coagulation factor VIII and correction of hemophilia A after in vivo retroviral gene transfer in factor VIII-deficient mice

Proceedings of the National Academy of Sciences of the United States of America

Volumn 96, Issue 18, 1999, Pages 10379-10384

  VandenDriessche, Thierry ^a   Vanslembrouck, Veerle ^a   Goovaerts, Inge ^a   Zwinnen, Hans ^a   Vanderhaeghen, Marie Line ^b   Collen, Desire ^a   Chuah, Marinee K L ^a  

^a DEPARTMENT OF PLANT SYSTEMS BIOLOGY   (Belgium)

^b FREE UNIVERSITY OF BRUSSELS   (Belgium)

Author keywords

Gene therapy; Pseudotyping; Retroviral vector

Indexed keywords

BLOOD CLOTTING FACTOR 8; BLOOD CLOTTING FACTOR 8 INHIBITOR; VIRUS GLYCOPROTEIN; VIRUS VECTOR;

ANIMAL CELL; ANIMAL MODEL; ARTICLE; GENE EXPRESSION; GENE THERAPY; GENE TRANSFER; HEMOPHILIA A; LIVER; MOUSE; NEWBORN; NONHUMAN; PRIORITY JOURNAL; RETROVIRUS; VIRUS TYPING;

ANIMALS; FACTOR VIII; GENE THERAPY; GENE TRANSFER TECHNIQUES; HEMOPHILIA A; HUMANS; MEMBRANE GLYCOPROTEINS; MICE; MICE, KNOCKOUT; ORGAN SPECIFICITY; PHENOTYPE; POLYMERASE CHAIN REACTION; RETROVIRIDAE; RNA, MESSENGER; TIME FACTORS; TRANSCRIPTION, GENETIC; VESICULAR STOMATITIS-INDIANA VIRUS; VIRAL ENVELOPE PROTEINS;

ANIMALIA; UNIDENTIFIED RETROVIRUS; VESICULAR STOMATITIS VIRUS;

EID: 0033621126     PISSN: 00278424     EISSN: None     Source Type: Journal    
DOI: 10.1073/pnas.96.18.10379     Document Type: Article

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