Friedreich's ataxia induced pluripotent stem cells model intergenerational GAATTC triplet repeat instability

Cell Stem Cell

Volumn 7, Issue 5, 2010, Pages 631-637

  Ku, Sherman ^a   Soragni, Elisabetta ^a   Campau, Erica ^a   Thomas, Elizabeth A ^a   Altun, Gulsah ^a   Laurent, Louise C ^a,b   Loring, Jeanne F ^a   Napierala, Marek ^c   Gottesfeld, Joel M ^a  

^a SCRIPPS RESEARCH INSTITUTE   (United States)

^b UNIVERSITY OF CALIFORNIA   (United States)

^c UNIVERSITY OF TEXAS MD ANDERSON CANCER CENTER   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

PROTEIN MSH2; SHORT HAIRPIN RNA; TRANSCRIPTION FACTOR;

ARTICLE; FIBROBLAST; FRIEDREICH ATAXIA; FXN GENE; GENE; GENE EXPRESSION; GENE SILENCING; GENOMIC INSTABILITY; HUMAN; HUMAN CELL; INTRON; NUCLEAR REPROGRAMMING; NUCLEOTIDE SEQUENCE; PLURIPOTENT STEM CELL; PRIORITY JOURNAL;

CELLS, CULTURED; DNA REPEAT EXPANSION; FRIEDREICH ATAXIA; HUMANS; INDUCED PLURIPOTENT STEM CELLS; IRON-BINDING PROTEINS; MICROSATELLITE INSTABILITY; TRINUCLEOTIDE REPEAT EXPANSION;

EID: 78049512763     PISSN: 19345909     EISSN: None     Source Type: Journal    
DOI: 10.1016/j.stem.2010.09.014     Document Type: Article

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