Ocular gene therapy: An evaluation of recombinant adeno-associated virus-mediated gene therapy interventions for the treatment of ocular disease

Human Gene Therapy

Volumn 21, Issue 8, 2010, Pages 915-927

  Roy, Kamolika ^a   Stein, Linda ^a   Kaushal, Shalesh ^a  

^a UNIVERSITY OF MASSACHUSETTS MEDICAL SCHOOL   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ADENOVIRUS VECTOR; RECOMBINANT ADENO ASSOCIATED VIRAL VECTOR; UNCLASSIFIED DRUG;

AUTOSOMAL DOMINANT DISORDER; AUTOSOMAL RECESSIVE DISORDER; BARDET BIEDL SYNDROME; COLOR BLINDNESS; CORNEA DISEASE; CORNEA NEOVASCULARIZATION; DIABETIC RETINOPATHY; DRUG SCREENING; GENE TARGETING; GENE THERAPY; HUMAN; LEBER CONGENITAL AMAUROSIS; MULTIPLE SCLEROSIS; OPEN ANGLE GLAUCOMA; RETINA CONE; RETINA DISEASE; RETINA MACULA AGE RELATED DEGENERATION; RETINA NEOVASCULARIZATION; RETINA ROD; RETINITIS PIGMENTOSA; RETINOSCHISIS; REVIEW; USHER SYNDROME;

ANIMALS; DEPENDOVIRUS; FEMALE; GENE THERAPY; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; HUMANS; MALE; MODELS, ANIMAL; RECOMBINANT PROTEINS; RETINAL DISEASES; SAIMIRI; VISION, OCULAR;

ADENO-ASSOCIATED VIRUS; ANIMALIA;

EID: 77955499196     PISSN: 10430342     EISSN: None     Source Type: Journal    
DOI: 10.1089/hum.2010.041     Document Type: Review

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