Successful treatment of metachromatic leukodystrophy using bone marrow transplantation of HoxB4 overexpressing cells

Molecular Therapy

Volumn 18, Issue 7, 2010, Pages 1373-1378

  Miyake, Noriko ^a   Miyake, Koichi ^a   Karlsson, Stefan ^b   Shimada, Takashi ^a  

^a NIPPON MEDICAL SCHOOL   (Japan)

^b LUND UNIVERSITY   (Sweden)

Author keywords

[No Author keywords available]

Indexed keywords

ALCIAN BLUE; GREEN FLUORESCENT PROTEIN; TRANSCRIPTION FACTOR; TRANSCRIPTION FACTOR HOXB4; UNCLASSIFIED DRUG;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; BONE MARROW TRANSPLANTATION; BRAIN TISSUE; CAPSULA INTERNA; CELL BASED GENE THERAPY; CELL DIFFERENTIATION; CELL PROLIFERATION; CONTROLLED STUDY; CORPUS CALLOSUM; DISEASE COURSE; DISEASE MODEL; EXPERIMENTAL MOUSE; GENE IDENTIFICATION; GENE OVEREXPRESSION; GENETIC TRANSFECTION; IMMUNOHISTOCHEMISTRY; METACHROMATIC LEUKODYSTROPHY; MOUSE; NONHUMAN; OLIGODENDROGLIA; SIGNAL TRANSDUCTION;

ANIMALS; BONE MARROW CELLS; BONE MARROW TRANSPLANTATION; FLOW CYTOMETRY; HOMEODOMAIN PROTEINS; HUMANS; IMMUNOHISTOCHEMISTRY; LEUKODYSTROPHY, METACHROMATIC; MICE; MICE, INBRED C57BL; MICE, KNOCKOUT; REVERSE TRANSCRIPTASE POLYMERASE CHAIN REACTION;

ANIMALIA; MUS;

EID: 77954242057     PISSN: 15250016     EISSN: 15250024     Source Type: Journal    
DOI: 10.1038/mt.2010.74     Document Type: Article

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