The status of hematopoietic stem cell transplantation in lysosomal storage disease

Pediatric Neurology

Volumn 29, Issue 5, 2003, Pages 391-403

  Malatack, J Jeffrey ^a,b   Consolini, Deborah M ^a   Bayever, Eliel ^c  

^a THOMAS JEFFERSON UNIVERSITY   (United States)

^b NEMOURS ALFRED I DUPONT HOSPITAL FOR CHILDREN   (United States)

^c PFIZER INC   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ARTICLE; BONE MARROW TRANSPLANTATION; CELL CULTURE; CLINICAL FEATURE; CLINICAL TRIAL; DIAGNOSTIC TEST; DISEASE MODEL; EXPERIMENTAL MODEL; GAUCHER DISEASE; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMAN; HUNTER SYNDROME; HURLER SYNDROME; IATROGENIC DISEASE; LYSOSOME STORAGE DISEASE; MAROTEAUX LAMY SYNDROME; METACHROMATIC LEUKODYSTROPHY; MORQUIO SYNDROME; NONHUMAN; PRIORITY JOURNAL; SANFILIPPO SYNDROME; SCREENING TEST; TREATMENT OUTCOME;

EID: 0346995457     PISSN: 08878994     EISSN: None     Source Type: Journal    
DOI: 10.1016/j.pediatrneurol.2003.09.003     Document Type: Review

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