Transgenic human α-hemoglobin stabilizing protein could partially relieve βiVS-2-654-thalassemia syndrome in model mice

Human Gene Therapy

Volumn 21, Issue 2, 2010, Pages 149-156

  Wang, Baobin ^a   Fang, Yudan ^a,b   Guo, Xinbing ^a,b   Ren, Zhaorui ^a   Zhang, Jingzhi ^a,b  

^a SHANGHAI JIAO TONG UNIVERSITY SCHOOL OF MEDICINE   (China)

^b BEIJING HOSPITAL   (China)

Author keywords

[No Author keywords available]

Indexed keywords

ALPHA HEMOGLOBIN STABILIZING PROTEIN; CHAPERONE; COMPLEMENTARY DNA; HEMOGLOBIN; LENTIVIRUS VECTOR; MESSENGER RNA; RECOMBINANT PROTEIN; UNCLASSIFIED DRUG;

ANEMIA; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; BETA THALASSEMIA; BONE MARROW; ERYTHROCYTE; EXTRAMEDULLARY HEMATOPOIESIS; GENE EXPRESSION; GENE THERAPY; HEMATOLOGICAL PARAMETERS; HEMOGLOBIN DETERMINATION; HISTOPATHOLOGY; HUMAN; LIVER; MEAN CORPUSCULAR HEMOGLOBIN; MEAN CORPUSCULAR VOLUME; MOUSE; NONHUMAN; REAL TIME POLYMERASE CHAIN REACTION; REVERSE TRANSCRIPTION POLYMERASE CHAIN REACTION; SPLEEN; SPLENOMEGALY; TRANSGENE; TRANSGENIC MOUSE; VIRAL GENE DELIVERY SYSTEM; WESTERN BLOTTING;

ANIMALS; BETA-THALASSEMIA; BLOOD PROTEINS; DISEASE MODELS, ANIMAL; ERYTHROCYTES; FEMALE; GENE THERAPY; HEMOGLOBINS; HETEROZYGOTE; HUMANS; MALE; MICE; MOLECULAR CHAPERONES; TRANSGENES; TREATMENT OUTCOME;

MUS;

EID: 77249105078     PISSN: 10430342     EISSN: None     Source Type: Journal    
DOI: 10.1089/hum.2009.132     Document Type: Article

References (21)

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