Lentiviral-mediated genetic correction of hematopoietic and mesenchymal progenitor cells from fanconi anemia patients

Molecular Therapy

Volumn 17, Issue 6, 2009, Pages 1083-1092

  Jacome, Ariana ^a   Navarro, Susana ^a   Río, Paula ^a   Yañez, Rosa M ^a   González Murillo, Africa ^a   Lozano, M Luz ^a   Lamana, Maria Luisa ^a   Sevilla, Julian ^b   Olive, Teresa ^c   Diaz Heredia, Cristina ^c   Badell, Isabel ^d   Estella, Jesus ^e   Madero, Luis ^b   Guenechea, Guillermo ^a   Casado, José ^a   Segovia, Jose C ^a   Bueren, Juan A ^a  

^a CIEMAT   (Spain)

^b HOSPITAL INFANTIL UNIVERSITARIO NIÑO JESÚS   (Spain)

^c HOSPITAL UNIVERSITARI VALL D HEBRON   (Spain)

^d HOSPITAL DE LA SANTA CREU I SANT PAU   (Spain)

^e Hospital San Joan de Deu   (Spain)

Author keywords

[No Author keywords available]

Indexed keywords

CD34 ANTIGEN; FANCONI ANEMIA GROUP A PROTEIN; HEMOGLOBIN; LENTIVIRUS VECTOR;

ARTICLE; BONE MARROW; CELL COUNT; CELL POPULATION; CLINICAL ARTICLE; COLONY FORMING CELL; CONTROLLED STUDY; CRYOPRESERVATION; ENGRAFTMENT; FANCONI ANEMIA; HEMATOPOIETIC STEM CELL; HUMAN; HUMAN CELL; HUMAN TISSUE; MESENCHYMAL STEM CELL; NEUTROPHIL COUNT; NONVIRAL GENE DELIVERY SYSTEM; PHENOTYPE; THROMBOCYTE COUNT; VIRAL GENE THERAPY;

ANTIGENS, CD34; BONE MARROW CELLS; CELL LINE; CELLS, CULTURED; FANCONI ANEMIA; GENETIC VECTORS; HEMATOPOIETIC STEM CELLS; HUMANS; LENTIVIRUS; MESENCHYMAL STEM CELLS;

EID: 67349229591     PISSN: 15250016     EISSN: 15250024     Source Type: Journal    
DOI: 10.1038/mt.2009.26     Document Type: Article

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