-
1
-
-
0034724857
-
Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease
-
Cavazzana-Calvo M, Hacein-Bey S, de Saint Basile G, et al. Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease. Science. 2000;288:669-672.
-
(2000)
Science
, vol.288
, pp. 669-672
-
-
Cavazzana-Calvo, M.1
Hacein-Bey, S.2
De Saint Basile, G.3
-
2
-
-
0025279872
-
Gene transfer by retrovirus vectors occurs only in cells that are actively replicating at the time of infection
-
Miller DG, Adam MA, Miller AD. Gene transfer by retrovirus vectors occurs only in cells that are actively replicating at the time of infection. Mol Cell Biol. 1990;10:4239-4242.
-
(1990)
Mol Cell Biol
, vol.10
, pp. 4239-4242
-
-
Miller, D.G.1
Adam, M.A.2
Miller, A.D.3
-
3
-
-
0027158091
-
Integration of murine leukemia virus DNA depends on mitosis
-
Roe T, Reynolds TC, Yu G, Brown PO. Integration of murine leukemia virus DNA depends on mitosis. EMBO J. 1993;12:2099-2108.
-
(1993)
EMBO J
, vol.12
, pp. 2099-2108
-
-
Roe, T.1
Reynolds, T.C.2
Yu, G.3
Brown, P.O.4
-
4
-
-
0029915482
-
High-resolution cell cycle analysis of defined phenotypic subsets within primitive human hematopoietic cell populations
-
Jordan CT, Yamasaki G, Minamoto D. High-resolution cell cycle analysis of defined phenotypic subsets within primitive human hematopoietic cell populations. Exp Hematol. 1996;24:1347-1355.
-
(1996)
Exp Hematol
, vol.24
, pp. 1347-1355
-
-
Jordan, C.T.1
Yamasaki, G.2
Minamoto, D.3
-
5
-
-
0036846846
-
Lentivirus-mediated gene transfer into hematopoietic repopulating cells in baboons
-
Horn PA, Morris JC, Bukovsky AA, et al. Lentivirus-mediated gene transfer into hematopoietic repopulating cells in baboons. Gene Ther. 2002;9:1464-1471.
-
(2002)
Gene Ther
, vol.9
, pp. 1464-1471
-
-
Horn, P.A.1
Morris, J.C.2
Bukovsky, A.A.3
-
6
-
-
0032529523
-
Ex vivo expansion of genetically marked Rhesus peripheral blood progenitor cells results in diminished long-term repopulating ability
-
Tisdale JF, Hanazono Y, Sellers SE, et al. Ex vivo expansion of genetically marked Rhesus peripheral blood progenitor cells results in diminished long-term repopulating ability. Blood. 1998;92:1131-1141.
-
(1998)
Blood
, vol.92
, pp. 1131-1141
-
-
Tisdale, J.F.1
Hanazono, Y.2
Sellers, S.E.3
-
7
-
-
0037108187
-
Gene therapy of Fanconi anemia: Preclinical efficacy using lentiviral vectors
-
Galimi F, Noll M, Kanazawa Y, et al. Gene therapy of Fanconi anemia: preclinical efficacy using lentiviral vectors. Blood. 2002;100:2732-2736.
-
(2002)
Blood
, vol.100
, pp. 2732-2736
-
-
Galimi, F.1
Noll, M.2
Kanazawa, Y.3
-
8
-
-
0029996147
-
In vivo gene delivery and stable transduction of nondividing cells by a lentiviral vector
-
Naldini L, Blömer U, Gallay P, et al. In vivo gene delivery and stable transduction of nondividing cells by a lentiviral vector. Science. 1996;272:263-267.
-
(1996)
Science
, vol.272
, pp. 263-267
-
-
Naldini, L.1
Blömer, U.2
Gallay, P.3
-
9
-
-
0028055281
-
Passage through mitosis is required for oncoretroviruses but not for the human immunodeficiency virus
-
Lewis PF, Emerman M. Passage through mitosis is required for oncoretroviruses but not for the human immunodeficiency virus. J Virol. 1994;68:510-516.
-
(1994)
J Virol
, vol.68
, pp. 510-516
-
-
Lewis, P.F.1
Emerman, M.2
-
10
-
-
0033532628
-
Cytokine signals are sufficient for HIV-1 infection of resting human T lymphocytes
-
Unutmaz D, KewalRamani VN, Marmon S, Littman DR. Cytokine signals are sufficient for HIV-1 infection of resting human T lymphocytes. J Exp Med. 1999;189:1735-1746.
-
(1999)
J Exp Med
, vol.189
, pp. 1735-1746
-
-
Unutmaz, D.1
KewalRamani, V.N.2
Marmon, S.3
Littman, D.R.4
-
11
-
-
0001221797
-
Marking and gene expression by a lentivirus vector in transplanted human and nonhuman primate CD34(+) cells
-
An DS, Wersto RP, Agricola BA, et al. Marking and gene expression by a lentivirus vector in transplanted human and nonhuman primate CD34(+) cells. J Virol. 2000;74:1286-1295.
-
(2000)
J Virol
, vol.74
, pp. 1286-1295
-
-
An, D.S.1
Wersto, R.P.2
Agricola, B.A.3
-
12
-
-
0035088020
-
Lentivirus vector-mediated hematopoietic stem cell gene transfer of common gamma-chain cytokine receptor in rhesus macaques
-
An DS, Kung SK, Bonifacino A, et al. Lentivirus vector-mediated hematopoietic stem cell gene transfer of common gamma-chain cytokine receptor in rhesus macaques. J Virol. 2001;75:3547-3555.
-
(2001)
J Virol
, vol.75
, pp. 3547-3555
-
-
An, D.S.1
Kung, S.K.2
Bonifacino, A.3
-
14
-
-
0037015007
-
Cellular inhibitors with Fv1-like activity restrict human and simian immunodeficiency virus tropism
-
Cowan S, Hatzlioannou T, Cunningham T, Muesing MA, Gottlinger HG, Bieniasz PD. Cellular inhibitors with Fv1-like activity restrict human and simian immunodeficiency virus tropism. Proc Natl Acad Sci U S A. 2002;99:11914-11919.
-
(2002)
Proc Natl Acad Sci U S A
, vol.99
, pp. 11914-11919
-
-
Cowan, S.1
Hatzlioannou, T.2
Cunningham, T.3
Muesing, M.A.4
Gottlinger, H.G.5
Bieniasz, P.D.6
-
15
-
-
0034040751
-
Gene transfer by lentiviral vectors is limited by nuclear translocation and rescued by HIV-1 pol sequences
-
Follenzi A, Ailles LE, Bakovic S, Geuna M, Naldini L. Gene transfer by lentiviral vectors is limited by nuclear translocation and rescued by HIV-1 pol sequences. Nat Genet. 2000;25:217-222.
-
(2000)
Nat Genet
, vol.25
, pp. 217-222
-
-
Follenzi, A.1
Ailles, L.E.2
Bakovic, S.3
Geuna, M.4
Naldini, L.5
-
16
-
-
0030819379
-
Multiply attenuated lentiviral vector achieves efficient gene delivery in vivo
-
Zufferey R, Nagy D, Mandel RJ, Naldini L, Trono D. Multiply attenuated lentiviral vector achieves efficient gene delivery in vivo. Nat Biotechnol. 1997;15:871-875.
-
(1997)
Nat Biotechnol
, vol.15
, pp. 871-875
-
-
Zufferey, R.1
Nagy, D.2
Mandel, R.J.3
Naldini, L.4
Trono, D.5
-
17
-
-
0035496914
-
Sustained multilineage gene persistence and expression in dogs transplanted with CD34(+) marrow cells transduced by RD114-pseudotype oncoretrovirus vectors
-
Goemer M, Horn PA, Peterson L, et al. Sustained multilineage gene persistence and expression in dogs transplanted with CD34(+) marrow cells transduced by RD114-pseudotype oncoretrovirus vectors. Blood. 2001;98:2065-2070.
-
(2001)
Blood
, vol.98
, pp. 2065-2070
-
-
Goemer, M.1
Horn, P.A.2
Peterson, L.3
-
18
-
-
0037105534
-
Pharmacologically regulated in vivo selection in a large animal
-
Neff T, Horn PA, Valli VE, et al. Pharmacologically regulated in vivo selection in a large animal. Blood. 2002;100:2026-2031.
-
(2002)
Blood
, vol.100
, pp. 2026-2031
-
-
Neff, T.1
Horn, P.A.2
Valli, V.E.3
-
20
-
-
0345144017
-
Clonality analysis after retroviral-mediated gene transfer to CD34(+) cells from the cord blood of ADA-deficient SCID neonates
-
Schmidt M, Carbonaro DA, Speckmann C, et al. Clonality analysis after retroviral-mediated gene transfer to CD34(+) cells from the cord blood of ADA-deficient SCID neonates. Nat Med. 2003;9:463-468.
-
(2003)
Nat Med
, vol.9
, pp. 463-468
-
-
Schmidt, M.1
Carbonaro, D.A.2
Speckmann, C.3
-
21
-
-
0037108189
-
Polyclonal long-term repopulating stem cell clones in a primate model
-
Schmidt M, Zickler P, Hoffmann G, et al. Polyclonal long-term repopulating stem cell clones in a primate model. Blood. 2002;100:2737-2743.
-
(2002)
Blood
, vol.100
, pp. 2737-2743
-
-
Schmidt, M.1
Zickler, P.2
Hoffmann, G.3
-
22
-
-
0942276849
-
Induction of cytotoxic T-lymphocyte responses to enhanced green and yellow fluorescent proteins after myeloablative conditioning
-
Morris JC, Conerly M, Thomasson B, Storek J, Riddell SR, Kiem H-P. Induction of cytotoxic T-lymphocyte responses to enhanced green and yellow fluorescent proteins after myeloablative conditioning. Blood. 2004;103:492-499.
-
(2004)
Blood
, vol.103
, pp. 492-499
-
-
Morris, J.C.1
Conerly, M.2
Thomasson, B.3
Storek, J.4
Riddell, S.R.5
Kiem, H.-P.6
-
23
-
-
0033215519
-
The use of granulocyte colony-stimulating factor during retroviral transduction on fibronectin fragment CH-296 enhances gene transfer into hematopoietic repopulating cells in dogs
-
Goemer M, Bruno B, McSweeney PA, Buron G, Storb R, Kiem H-P. The use of granulocyte colony-stimulating factor during retroviral transduction on fibronectin fragment CH-296 enhances gene transfer into hematopoietic repopulating cells in dogs. Blood. 1999;94:2287-2292.
-
(1999)
Blood
, vol.94
, pp. 2287-2292
-
-
Goemer, M.1
Bruno, B.2
McSweeney, P.A.3
Buron, G.4
Storb, R.5
Kiem, H.-P.6
-
24
-
-
0036892648
-
Highly efficient gene transfer into baboon marrow repopulating cells using GALV-pseudotype oncoretroviral vectors produced by human packaging cells
-
Horn PA, Topp MS, Morris JC, Riddell SR, Kiem H-P. Highly efficient gene transfer into baboon marrow repopulating cells using GALV-pseudotype oncoretroviral vectors produced by human packaging cells. Blood. 2002;100:3960-3967.
-
(2002)
Blood
, vol.100
, pp. 3960-3967
-
-
Horn, P.A.1
Topp, M.S.2
Morris, J.C.3
Riddell, S.R.4
Kiem, H.-P.5
-
25
-
-
0029859412
-
Improved retroviral gene transfer into murine and rhesus peripheral blood or bone marrow repopulating cells primed in vivo with stem cell factor and granulocyte colony-stimulating factor
-
Dunbar CE, Seidel NE, Doren S, et al. Improved retroviral gene transfer into murine and rhesus peripheral blood or bone marrow repopulating cells primed in vivo with stem cell factor and granulocyte colony-stimulating factor. Proc Natl Acad Sci U S A. 1996;93:11871-11876.
-
(1996)
Proc Natl Acad Sci U S A
, vol.93
, pp. 11871-11876
-
-
Dunbar, C.E.1
Seidel, N.E.2
Doren, S.3
-
26
-
-
0037443484
-
Retroviral transduction efficiency of G-CSF+SCF-mobilized peripheral blood CD34+ cells is superior to G-CSF or G-CSF+Flt3-L-mobilized cells in nonhuman primates
-
Hematti P, Sellars SE, Agricola BA, Metzger ME, Donahue RE, Dunbar CE. Retroviral transduction efficiency of G-CSF+SCF-mobilized peripheral blood CD34+ cells is superior to G-CSF or G-CSF+Flt3-L-mobilized cells in nonhuman primates. Blood. 2003;101:2199-2205.
-
(2003)
Blood
, vol.101
, pp. 2199-2205
-
-
Hematti, P.1
Sellars, S.E.2
Agricola, B.A.3
Metzger, M.E.4
Donahue, R.E.5
Dunbar, C.E.6
-
27
-
-
0035312983
-
Induction of cytotoxic T lymphocyte and antibody responses to enhanced green fluorescent protein following transplantation of transduced CD34(+) hematopoietic cells
-
Rosenzweig M, Connole M, Glickman R, et al. Induction of cytotoxic T lymphocyte and antibody responses to enhanced green fluorescent protein following transplantation of transduced CD34(+) hematopoietic cells. Blood. 2001;97:1951-1959.
-
(2001)
Blood
, vol.97
, pp. 1951-1959
-
-
Rosenzweig, M.1
Connole, M.2
Glickman, R.3
-
28
-
-
0029068059
-
Retrovirally marked CD34-enriched peripheral blood and bone marrow cells contribute to long-term engraftment after autologous transplantation
-
Dunbar CE, Cottler-Fox M, O'Shaughnessy JA, et al. Retrovirally marked CD34-enriched peripheral blood and bone marrow cells contribute to long-term engraftment after autologous transplantation. Blood. 1995;85:3048-3057.
-
(1995)
Blood
, vol.85
, pp. 3048-3057
-
-
Dunbar, C.E.1
Cottler-Fox, M.2
O'Shaughnessy, J.A.3
-
29
-
-
0345305289
-
Direct comparison of steady state marrow, primed marrow, and mobilized peripheral blood for transduction of hematopoietic stem cells in dogs
-
Thomasson B, Peterson L, Thompson J, Goemer M, Kiem H-P. Direct comparison of steady state marrow, primed marrow, and mobilized peripheral blood for transduction of hematopoietic stem cells in dogs. Hum Gene Ther. 2003;14:1683-1686.
-
(2003)
Hum Gene Ther
, vol.14
, pp. 1683-1686
-
-
Thomasson, B.1
Peterson, L.2
Thompson, J.3
Goemer, M.4
Kiem, H.-P.5
-
30
-
-
0031015915
-
The unexpected G0/G1 cell cycle status of mobilized hematopoietic stem cells from peripheral blood
-
Uchida N, He D, Friera AM, et al. The unexpected G0/G1 cell cycle status of mobilized hematopoietic stem cells from peripheral blood. Blood. 1997;89:465-472.
-
(1997)
Blood
, vol.89
, pp. 465-472
-
-
Uchida, N.1
He, D.2
Friera, A.M.3
-
31
-
-
0036270138
-
Peripheral blood stem cells differ from bone marrow stem cells in cell cycle status, repopulating potential, and sensitivity toward hyperthermic purging in mice mobilized with cyclophosphamide and granulocyte colony-stimulating factor
-
Wierenga PK, Setrolkromo R, Kamps G, Kampinga HH, Vellenga E. Peripheral blood stem cells differ from bone marrow stem cells in cell cycle status, repopulating potential, and sensitivity toward hyperthermic purging in mice mobilized with cyclophosphamide and granulocyte colony-stimulating factor. J Hematother Stem Cell Res. 2002;11:523-532.
-
(2002)
J Hematother Stem Cell Res
, vol.11
, pp. 523-532
-
-
Wierenga, P.K.1
Setrolkromo, R.2
Kamps, G.3
Kampinga, H.H.4
Vellenga, E.5
-
32
-
-
0033104973
-
No discrepancy between in vivo gene marking efficiency assessed in peripheral blood populations compared with bone marrow progenitors or CD34+ cells
-
Sellers SE, Tisdale JF, Bodine DM, et al. No discrepancy between in vivo gene marking efficiency assessed in peripheral blood populations compared with bone marrow progenitors or CD34+ cells. Hum Gene Ther. 1999;10:633-640.
-
(1999)
Hum Gene Ther
, vol.10
, pp. 633-640
-
-
Sellers, S.E.1
Tisdale, J.F.2
Bodine, D.M.3
-
33
-
-
0028864561
-
Engraftment of gene-modified umbilical cord blood cells in neonates with adenosine deaminase deficiency
-
Kohn DB, Weinberg KI, Nolta JA, et al. Engraftment of gene-modified umbilical cord blood cells in neonates with adenosine deaminase deficiency. Nat Med. 1995;1:1017-1023.
-
(1995)
Nat Med
, vol.1
, pp. 1017-1023
-
-
Kohn, D.B.1
Weinberg, K.I.2
Nolta, J.A.3
-
34
-
-
0029800108
-
Gene marking
-
Brenner M. Gene marking. Hum Gene Ther. 1996;7:1927-1936.
-
(1996)
Hum Gene Ther
, vol.7
, pp. 1927-1936
-
-
Brenner, M.1
-
35
-
-
0037448352
-
A serious adverse event after successful gene therapy for X-linked severe combined immunodeficiency
-
Hacein-Bey-Abina S, von Kalle C, Schmidt M, et al. A serious adverse event after successful gene therapy for X-linked severe combined immunodeficiency. N Engl J Med. 2003;348:255-256.
-
(2003)
N Engl J Med
, vol.348
, pp. 255-256
-
-
Hacein-Bey-Abina, S.1
Von Kalle, C.2
Schmidt, M.3
-
36
-
-
0037443457
-
Side effects of retroviral gene transfer into hematopoietic stem cells
-
Baum C, Düllmann J, Li Z, et al. Side effects of retroviral gene transfer into hematopoietic stem cells. Blood. 2003;101:2099-2114.
-
(2003)
Blood
, vol.101
, pp. 2099-2114
-
-
Baum, C.1
Düllmann, J.2
Li, Z.3
-
37
-
-
0021835658
-
Insertion mutagenesis of embryonal carcinoma cells by retroviruses
-
King W, Patel MD, Lobel LI, Goff SP, Nguyen-Huu MC. Insertion mutagenesis of embryonal carcinoma cells by retroviruses. Science. 1985;228:554-558.
-
(1985)
Science
, vol.228
, pp. 554-558
-
-
King, W.1
Patel, M.D.2
Lobel, L.I.3
Goff, S.P.4
Nguyen-Huu, M.C.5
-
38
-
-
0027421669
-
Distinct classes of factor-independent mutants can be isolated after retroviral mutagenesis of a human myeloid stem cell line
-
Stocking C, Bergholz U, Friel J, et al. Distinct classes of factor-independent mutants can be isolated after retroviral mutagenesis of a human myeloid stem cell line. Growth Factors. 1993;8:197-209.
-
(1993)
Growth Factors
, vol.8
, pp. 197-209
-
-
Stocking, C.1
Bergholz, U.2
Friel, J.3
-
39
-
-
0037441587
-
Lentiviral vector transduction of NOD/SCID repopulating cells results in multiple vector integrations per transduced cell: Risk of insertional mutagenesis
-
Woods NB, Muessig A, Schmidt M, et al. Lentiviral vector transduction of NOD/SCID repopulating cells results in multiple vector integrations per transduced cell: risk of insertional mutagenesis. Blood. 2003;101:1284-1289.
-
(2003)
Blood
, vol.101
, pp. 1284-1289
-
-
Woods, N.B.1
Muessig, A.2
Schmidt, M.3
|