Gene therapy of βc-deficient pulmonary alveolar proteinosis (βc-PAP): Studies in a murine in vivo model

Molecular Therapy

Volumn 16, Issue 4, 2008, Pages 757-764

  Kleff, Veronika ^a   Sorg, Ursula R ^a   Bury, Carsten ^b   Suzuki, Takuji ^c   Rattmann, Ina ^a,c   Jerabek Willemsen, Moran ^a,c   Poremba, Christopher ^d   Flasshove, Michael ^a   Opalka, Bertram ^a   Trapnell, Bruce ^c   Dirksen, Uta ^b   Moritz, Thomas ^a,c  

^a UNIVERSITY HOSPITAL ESSEN   (Germany)

^b UNIVERSITY OF MÜNSTER   (Germany)

^c CINCINNATI CHILDREN'S HOSPITAL MEDICAL CENTER   (United States)

^d HEINRICH HEINE UNIVERSITY   (Germany)

Author keywords

[No Author keywords available]

Indexed keywords

GRANULOCYTE MACROPHAGE COLONY STIMULATING FACTOR RECEPTOR; INTERLEUKIN 3 RECEPTOR; INTERLEUKIN 5 RECEPTOR; RETROVIRUS VECTOR;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; BETA CHAIN; BONE MARROW CELL; CONTROLLED STUDY; GENE CONSTRUCT; GENE EXPRESSION; GENE TRANSFER; GENETIC TRANSDUCTION; HEMATOPOIETIC STEM CELL; IN VITRO STUDY; IN VIVO STUDY; LUNG ALVEOLUS PROTEINOSIS; MOUSE; NONHUMAN; STEM CELL GENE THERAPY; VIRAL GENE DELIVERY SYSTEM; WILD TYPE;

MURINAE; MUS;

EID: 41149139870     PISSN: 15250016     EISSN: 15250024     Source Type: Journal    
DOI: 10.1038/mt.2008.7     Document Type: Article

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