Correction of sickle cell disease by homologous recombination in embryonic stem cells

Blood

Volumn 108, Issue 4, 2006, Pages 1183-1188

  Wu, Li Chen ^a   Sun, Chiao Wang ^a   Ryan, Thomas M ^a   Pawlik, Kevin M ^a   Ren, Jinxiang ^a   Townes, Tim M ^a  

^a UNIVERSITY OF ALABAMA AT BIRMINGHAM   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ANEMIA; ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; CONTROLLED STUDY; EMBRYONIC STEM CELL; GENE DUPLICATION; GENE MUTATION; GENE REPLACEMENT THERAPY; GENE TARGETING; GLOBIN GENE; HEMATOLOGY; HOMOLOGOUS RECOMBINATION; KIDNEY; KIDNEY FUNCTION; LIVER; MORPHOLOGY; MOUSE; NONHUMAN; PLASMID; PRIORITY JOURNAL; SICKLE CELL ANEMIA; SPLEEN;

EID: 33747152507     PISSN: 00064971     EISSN: 00064971     Source Type: Journal    
DOI: 10.1182/blood-2006-02-004812     Document Type: Article

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