-
1
-
-
0033974016
-
Latest developments in gene transfer technology: Achievements, perspectives, and controversies over therapeutic applications
-
Romano, G., Micheli, P., Pacilio, C. and Giordano, A. Latest developments in gene transfer technology: Achievements, perspectives, and controversies over therapeutic applications. Stem Cells 2000, 18: 19-39.
-
(2000)
Stem Cells
, vol.18
, pp. 19-39
-
-
Romano, G.1
Micheli, P.2
Pacilio, C.3
Giordano, A.4
-
2
-
-
0032798121
-
Gene transfer technology in therapy: Current applications and future goals
-
Romano, G., Pacilio, C. and Giordano, A. Gene transfer technology in therapy: Current applications and future goals. Stem Cells 1999, 17: 191-202.
-
(1999)
Stem Cells
, vol.17
, pp. 191-202
-
-
Romano, G.1
Pacilio, C.2
Giordano, A.3
-
3
-
-
0141728485
-
Gene transfer in experimental medicine
-
Romano, G. Gene transfer in experimental medicine. Drug News Perspect 2003, 16: 267-76.
-
(2003)
Drug News Perspect
, vol.16
, pp. 267-276
-
-
Romano, G.1
-
4
-
-
18744396940
-
Current development of lentiviral-mediated gene transfer
-
Romano, G. Current development of lentiviral-mediated gene transfer. Drugs News Perspect 2005, 18: 128-34.
-
(2005)
Drugs News Perspect
, vol.18
, pp. 128-134
-
-
Romano, G.1
-
5
-
-
0037143294
-
Clinical protocol. Gene therapy of Canavan disease: AAV-2 vector for neurosurgical delivery of aspartoacylase gene (ASPA) to the human brain
-
Janson, C., McPhee, S., Bilaniuk, L. et al. Clinical protocol. Gene therapy of Canavan disease: AAV-2 vector for neurosurgical delivery of aspartoacylase gene (ASPA) to the human brain. Hum Gene Ther 2002, 13: 1391-412.
-
(2002)
Hum Gene Ther
, vol.13
, pp. 1391-1412
-
-
Janson, C.1
McPhee, S.2
Bilaniuk, L.3
-
6
-
-
23844448882
-
Gene therapy for Parkinson's disease
-
Lawlor, P.A. and During, M.J. Gene therapy for Parkinson's disease. Expert Rev Mol Med 2004, 2004: 1-18.
-
(2004)
Expert Rev Mol Med
, vol.2004
, pp. 1-18
-
-
Lawlor, P.A.1
During, M.J.2
-
7
-
-
0035574739
-
Excitement in gene therapy
-
Anderson, W.F. Excitement in gene therapy. Hum Gene Ther 2001, 12: 1483-4.
-
(2001)
Hum Gene Ther
, vol.12
, pp. 1483-1484
-
-
Anderson, W.F.1
-
8
-
-
0038488551
-
Phase I trial of intranasal and endobronchial administration of a recombinant adeno-associated virus serotype 2 (rAAV2)-CFTR vector in adult cystic fibrosis patients: A two-part clinical study
-
Flotte, T.R., Zeitlin, P.L., Reynolds, T.C. et al. Phase I trial of intranasal and endobronchial administration of a recombinant adeno-associated virus serotype 2 (rAAV2)-CFTR vector in adult cystic fibrosis patients: A two-part clinical study. Hum Gene Ther 2003, 14: 1079-88.
-
(2003)
Hum Gene Ther
, vol.14
, pp. 1079-1088
-
-
Flotte, T.R.1
Zeitlin, P.L.2
Reynolds, T.C.3
-
9
-
-
0036377851
-
A phase II, double-blind, randomized, placebo-controlled clinical trial of tgAAVCF using maxillary sinus delivery in patients with cystic fibrosis with antrostomies
-
Wagner, J.A., Nepomuceno, I.B., Messner, A.H. et al. A phase II, double-blind, randomized, placebo-controlled clinical trial of tgAAVCF using maxillary sinus delivery in patients with cystic fibrosis with antrostomies. Hum Gene Ther 2002, 13: 1349-59.
-
(2002)
Hum Gene Ther
, vol.13
, pp. 1349-1359
-
-
Wagner, J.A.1
Nepomuceno, I.B.2
Messner, A.H.3
-
10
-
-
0034779927
-
A phase I study of aerosolized administration of tgAAVCF to cystic fibrosis subjects with mild lung disease
-
Aitken, M.L., Moss, R.B., Waltz, D.A. et al. A phase I study of aerosolized administration of tgAAVCF to cystic fibrosis subjects with mild lung disease. Hum Gene Ther 2001, 12: 1907-16.
-
(2001)
Hum Gene Ther
, vol.12
, pp. 1907-1916
-
-
Aitken, M.L.1
Moss, R.B.2
Waltz, D.A.3
-
11
-
-
0034050904
-
Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector
-
Kay, M.A., Manno, C.S., Ragni, M.V. et al. Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector. Nat Genet 2000, 24: 257-61.
-
(2000)
Nat Genet
, vol.24
, pp. 257-261
-
-
Kay, M.A.1
Manno, C.S.2
Ragni, M.V.3
-
12
-
-
0013442744
-
AAV-mediated factor IX gene transfer to skeletal muscle in patients with severe hemophilia B
-
Manno, C.S., Chew, A.J., Hutchinson, S. et al. AAV-mediated factor IX gene transfer to skeletal muscle in patients with severe hemophilia B. Blood 2003, 101: 2963-72.
-
(2003)
Blood
, vol.101
, pp. 2963-2972
-
-
Manno, C.S.1
Chew, A.J.2
Hutchinson, S.3
-
13
-
-
0742307402
-
Phase I trial of intramuscular injection of a recombinant adeno-associated virus alpha1-antitrypsin (rAAV2-CB-hAAT) gene vector to AAT-deficient adults
-
Flotte, T.R., Brantly, M.L., Spencer, L.T. et al. Phase I trial of intramuscular injection of a recombinant adeno-associated virus alpha1-antitrypsin (rAAV2-CB-hAAT) gene vector to AAT-deficient adults. Hum Gene Ther 2004, 15: 93-128.
-
(2004)
Hum Gene Ther
, vol.15
, pp. 93-128
-
-
Flotte, T.R.1
Brantly, M.L.2
Spencer, L.T.3
-
14
-
-
0014355039
-
Epidemiology of adenovirus-associated virus infection in a nursery population
-
Blacklow, N.R., Hoggan, M.D., Kapikian, A.Z. et al. Epidemiology of adenovirus-associated virus infection in a nursery population. Am J Epidemiol 1968, 88: 368-78.
-
(1968)
Am J Epidemiol
, vol.88
, pp. 368-378
-
-
Blacklow, N.R.1
Hoggan, M.D.2
Kapikian, A.Z.3
-
15
-
-
0022481276
-
Vaccinia virus, herpes simplex virus, and carcinogens induce DNA amplification in a human cell line and support replication of a helper-virus dependent parvovirus
-
Schlehofer, J.R., Ehrbar, M., zur Hausen, H. Vaccinia virus, herpes simplex virus, and carcinogens induce DNA amplification in a human cell line and support replication of a helper-virus dependent parvovirus. Virology 1986, 152: 110-7.
-
(1986)
Virology
, vol.152
, pp. 110-117
-
-
Schlehofer, J.R.1
Ehrbar, M.2
Zur Hausen, H.3
-
16
-
-
0016678424
-
Detection of adeno-associated virus (AAV)-specific nucleotide sequences in DNA isolated from latently infected Detroit 6 cells
-
Berns, K.I., Pinkerton, T.C., Thomas, G.F. et al. Detection of adeno-associated virus (AAV)-specific nucleotide sequences in DNA isolated from latently infected Detroit 6 cells. Virology 1975, 68: 556-60.
-
(1975)
Virology
, vol.68
, pp. 556-560
-
-
Berns, K.I.1
Pinkerton, T.C.2
Thomas, G.F.3
-
17
-
-
0028060363
-
Efficient gene transfer into nondividing cells by adeno-associated virus-based vectors
-
Podsakoff, G., Wong, K.K., Jr. and Chatterjee, S. Efficient gene transfer into nondividing cells by adeno-associated virus-based vectors. J Virol 1994, 68: 5656-66.
-
(1994)
J Virol
, vol.68
, pp. 5656-5666
-
-
Podsakoff, G.1
Wong Jr., K.K.2
Chatterjee, S.3
-
18
-
-
0028577595
-
Adeno-associated virus vectors preferentially transduce cells in S phase
-
Russell, D.W., Miller, A.D. and Alexander, I.E. Adeno-associated virus vectors preferentially transduce cells in S phase. Proc Natl Acad Sci USA 1994, 91: 8915-9.
-
(1994)
Proc Natl Acad Sci USA
, vol.91
, pp. 8915-8919
-
-
Russell, D.W.1
Miller, A.D.2
Alexander, I.E.3
-
19
-
-
2642539509
-
Gene therapy progress and prospects: Recombinant adeno-associated virus (rAAV) vectors
-
Flotte, T.R. Gene therapy progress and prospects: Recombinant adeno-associated virus (rAAV) vectors. Gene Ther 2004, 11: 805-10.
-
(2004)
Gene Ther
, vol.11
, pp. 805-810
-
-
Flotte, T.R.1
-
20
-
-
0037947557
-
Adeno-associated viruses undergo substantial evolution in primates during natural infections
-
Gao, G., Alvira, M.R., Somanathan, S. et al. Adeno-associated viruses undergo substantial evolution in primates during natural infections. Proc Natl Acad Sci USA 2003, 100: 6081-6.
-
(2003)
Proc Natl Acad Sci USA
, vol.100
, pp. 6081-6086
-
-
Gao, G.1
Alvira, M.R.2
Somanathan, S.3
-
21
-
-
0032959311
-
Cloning and characterization of adeno-associated virus type 5
-
Chiorini, J.A., Kim, F., Yang, L. and Kotin, R.M. Cloning and characterization of adeno-associated virus type 5. J Virol 1999, 73: 1309-19.
-
(1999)
J Virol
, vol.73
, pp. 1309-1319
-
-
Chiorini, J.A.1
Kim, F.2
Yang, L.3
Kotin, R.M.4
-
22
-
-
0030841312
-
Cloning of adeno-associated virus type 4 (AAV4) and generation of recombinant AAV4 particles
-
Chiorini, J.A., Yang, L., Liu, Y. et al. Cloning of adeno-associated virus type 4 (AAV4) and generation of recombinant AAV4 particles. J Virol 1997, 71: 6823-33.
-
(1997)
J Virol
, vol.71
, pp. 6823-6833
-
-
Chiorini, J.A.1
Yang, L.2
Liu, Y.3
-
23
-
-
0031984786
-
Infectious clones and vectors derived from adeno-associated virus (AAV) serotypes other than AAV type 2
-
Rutledge, E.A., Halbert, C.L. and Russell, D.W. Infectious clones and vectors derived from adeno-associated virus (AAV) serotypes other than AAV type 2. J Virol 1998, 72: 309-19.
-
(1998)
J Virol
, vol.72
, pp. 309-319
-
-
Rutledge, E.A.1
Halbert, C.L.2
Russell, D.W.3
-
24
-
-
0032924185
-
Gene therapy vectors based on adeno-associated virus type 1
-
Xiao, W., Chirmule, N., Berta, S.C. et al. Gene therapy vectors based on adeno-associated virus type 1. J Virol 1999, 73: 3994-4003.
-
(1999)
J Virol
, vol.73
, pp. 3994-4003
-
-
Xiao, W.1
Chirmule, N.2
Berta, S.C.3
-
25
-
-
0031906147
-
Membrane-associated heparan sulfate proteoglycan is a receptor for adeno-associated virus type 2 virions
-
Summerford, C. and Samulski, R.J. Membrane-associated heparan sulfate proteoglycan is a receptor for adeno-associated virus type 2 virions. J Virol 1998, 72: 1438-45.
-
(1998)
J Virol
, vol.72
, pp. 1438-1445
-
-
Summerford, C.1
Samulski, R.J.2
-
26
-
-
0032589751
-
AlphaVbeta5 integrin: A co-receptor for adeno-associated virus type 2 infection
-
Summerford, C., Bartlett, J.S., Samulski, R.J. AlphaVbeta5 integrin: A co-receptor for adeno-associated virus type 2 infection. Nat Med 1999, 5: 78-82.
-
(1999)
Nat Med
, vol.5
, pp. 78-82
-
-
Summerford, C.1
Bartlett, J.S.2
Samulski, R.J.3
-
27
-
-
0033010884
-
Human fibroblast growth factor receptor 1 is a co-receptor for infection by adeno-associated virus 2
-
Qing, K., Mah, C., Hansen, J. et al. Human fibroblast growth factor receptor 1 is a co-receptor for infection by adeno-associated virus 2. Nat Med 1999, 5: 71-7.
-
(1999)
Nat Med
, vol.5
, pp. 71-77
-
-
Qing, K.1
Mah, C.2
Hansen, J.3
-
28
-
-
0034957168
-
Adeno-associated virus serotype 4 (AAV4) and AAV5 both require sialic acid binding for hemagglutination and efficient transduction but differ in sialic acid linkage specificity
-
Kaludov, N., Brown, K.E., Walters, R.W. et al. Adeno-associated virus serotype 4 (AAV4) and AAV5 both require sialic acid binding for hemagglutination and efficient transduction but differ in sialic acid linkage specificity. J Virol 2001, 75: 6884-93.
-
(2001)
J Virol
, vol.75
, pp. 6884-6893
-
-
Kaludov, N.1
Brown, K.E.2
Walters, R.W.3
-
29
-
-
0034026085
-
Adeno-associated virus type 5 (AAV5) but not AAV2 binds to the apical surfaces of airway epithelia and facilitates gene transfer
-
Zabner, J., Seiler, M., Walters, R. et al. Adeno-associated virus type 5 (AAV5) but not AAV2 binds to the apical surfaces of airway epithelia and facilitates gene transfer. J Virol 2000, 74: 3852-8.
-
(2000)
J Virol
, vol.74
, pp. 3852-3858
-
-
Zabner, J.1
Seiler, M.2
Walters, R.3
-
30
-
-
0024322243
-
Organization of adeno-associated virus DNA in latently infected Detroit 6 cells
-
Kotin, R.M. and Berns, K.I. Organization of adeno-associated virus DNA in latently infected Detroit 6 cells. Virology 1989, 170: 460-7.
-
(1989)
Virology
, vol.170
, pp. 460-467
-
-
Kotin, R.M.1
Berns, K.I.2
-
31
-
-
0025214094
-
Site-specific integration by adeno-associated virus
-
Kotin, R.M., Siniscalsco, M., Samulski, R.J. et al. Site-specific integration by adeno-associated virus. Proc Natl Acad Sci USA 1990, 87: 2211-5.
-
(1990)
Proc Natl Acad Sci USA
, vol.87
, pp. 2211-2215
-
-
Kotin, R.M.1
Siniscalsco, M.2
Samulski, R.J.3
-
32
-
-
0027092001
-
Characterization of a preferred site on human chromosome 19q for integration of adeno-associated virus DNA by non-homologous recombination
-
Kotin, R.M., Linden, R.M. and Berns, K.I. Characterization of a preferred site on human chromosome 19q for integration of adeno-associated virus DNA by non-homologous recombination. EMBO J 1992, 11: 5071-8.
-
(1992)
EMBO J
, vol.11
, pp. 5071-5078
-
-
Kotin, R.M.1
Linden, R.M.2
Berns, K.I.3
-
33
-
-
0025721086
-
Mapping and direct visualization of a region-specific viral DNA integration site on chromosome 19q13-qter
-
Kotin R.M., Menninger, J.C., Ward, D.C. et al. Mapping and direct visualization of a region-specific viral DNA integration site on chromosome 19q13-qter. Genomics 1991, 10: 831-4.
-
(1991)
Genomics
, vol.10
, pp. 831-834
-
-
Kotin, R.M.1
Menninger, J.C.2
Ward, D.C.3
-
34
-
-
0026070440
-
Targeted integration of adeno-associated virus (AAV) into human chromosome 19
-
Samulski, R.J., Zhu, X., Xiao, X. et al. Targeted integration of adeno-associated virus (AAV) into human chromosome 19. EMBO J 1991, 10: 3941-50.
-
(1991)
EMBO J
, vol.10
, pp. 3941-3950
-
-
Samulski, R.J.1
Zhu, X.2
Xiao, X.3
-
35
-
-
0036678455
-
The atomic structure of adeno-associated virus (AAV-2), a vector for human gene therapy
-
Xie, Q., Bu, W., Bhatia, S. et al. The atomic structure of adeno-associated virus (AAV-2), a vector for human gene therapy. Proc Natl Acad Sci USA 2002, 99: 10405-10.
-
(2002)
Proc Natl Acad Sci USA
, vol.99
, pp. 10405-10410
-
-
Xie, Q.1
Bu, W.2
Bhatia, S.3
-
36
-
-
0035976603
-
Real-time single-molecule imaging of the infection pathway of an adeno-associated virus
-
Seisenberger, G., Ried, M.U., Endress, T. et al. Real-time single-molecule imaging of the infection pathway of an adeno-associated virus. Science 2001, 294: 1929-32.
-
(2001)
Science
, vol.294
, pp. 1929-1932
-
-
Seisenberger, G.1
Ried, M.U.2
Endress, T.3
-
37
-
-
0033998692
-
Infectious entry pathway of adeno-associated virus and adeno-associated virus vectors
-
Bartlett, J.S., Wilcher, R. and Samulski, R.J. Infectious entry pathway of adeno-associated virus and adeno-associated virus vectors. J Virol 2000, 74: 2777-85.
-
(2000)
J Virol
, vol.74
, pp. 2777-2785
-
-
Bartlett, J.S.1
Wilcher, R.2
Samulski, R.J.3
-
38
-
-
0028036513
-
Induction of mutant dynamin specifically blocks endocytic coated vesicle formation
-
Damke, H., Baba, T., Warnock, D.E. et al. Induction of mutant dynamin specifically blocks endocytic coated vesicle formation. J Cell Biol 1994, 127: 915-34.
-
(1994)
J Cell Biol
, vol.127
, pp. 915-934
-
-
Damke, H.1
Baba, T.2
Warnock, D.E.3
-
39
-
-
0028898261
-
Dynamin self-assembles into rings suggesting a mechanism for coated vesicle budding
-
Hinshaw, J.E. and Schmid, S.L. Dynamin self-assembles into rings suggesting a mechanism for coated vesicle budding. Nature 1995, 374: 190-2.
-
(1995)
Nature
, vol.374
, pp. 190-192
-
-
Hinshaw, J.E.1
Schmid, S.L.2
-
40
-
-
0028923349
-
Tubular membrane invaginations coated by dynamin rings are induced by GTP-gammaS in nerve terminals
-
Takey, K., McPherson, P.S., Schmid, S.L. and Camilli, P.D. Tubular membrane invaginations coated by dynamin rings are induced by GTP-gammaS in nerve terminals. Nature 1995, 374: 186-90.
-
(1995)
Nature
, vol.374
, pp. 186-190
-
-
Takey, K.1
McPherson, P.S.2
Schmid, S.L.3
Camilli, P.D.4
-
41
-
-
0033987571
-
Impaired intracellular trafficking of adeno-associated virus type 2 vectors limits efficient transduction of murine fibroblasts
-
Hansen, J., Qing, K., Kwon, H.J. et al. Impaired intracellular trafficking of adeno-associated virus type 2 vectors limits efficient transduction of murine fibroblasts. J Virol 2000, 74: 992-6.
-
(2000)
J Virol
, vol.74
, pp. 992-996
-
-
Hansen, J.1
Qing, K.2
Kwon, H.J.3
-
42
-
-
0036253749
-
Obstacles to human hematopoietic stem cell transduction by recombinant adeno-associated virus 2 vectors
-
Srivastava, A. Obstacles to human hematopoietic stem cell transduction by recombinant adeno-associated virus 2 vectors. J Cell Biochem Suppl 2002, 38: 39-45.
-
(2002)
J Cell Biochem Suppl
, vol.38
, pp. 39-45
-
-
Srivastava, A.1
-
43
-
-
0034091579
-
Endosomal processing limits gene transfer to polarized airway epithelia by adeno-associated virus
-
Duan, D., Yue, Y., Yan, Z. et al. Endosomal processing limits gene transfer to polarized airway epithelia by adeno-associated virus. J Clin Invest 2000, 105: 1573-87.
-
(2000)
J Clin Invest
, vol.105
, pp. 1573-1587
-
-
Duan, D.1
Yue, Y.2
Yan, Z.3
-
44
-
-
0036171821
-
Ubiquitination of both adeno-associated virus type 2 and 5 capsid proteins affects the transduction efficiency of recombinant vectors
-
Yan, Z., Zak, R., Gant Luxon, G.W. et al. Ubiquitination of both adeno-associated virus type 2 and 5 capsid proteins affects the transduction efficiency of recombinant vectors. J Virol 2002, 76: 2043-53.
-
(2002)
J Virol
, vol.76
, pp. 2043-2053
-
-
Yan, Z.1
Zak, R.2
Gant Luxon, G.W.3
-
45
-
-
0034849529
-
Adeno-associated virus type 2-mediated gene transfer: Role of cellular FKBP52 protein in transgene expression
-
Qing, K., Hansen, J., Weigel-Kelley, K.A. et al. Adeno-associated virus type 2-mediated gene transfer: Role of cellular FKBP52 protein in transgene expression. J Virol 2001, 75: 8968-76.
-
(2001)
J Virol
, vol.75
, pp. 8968-8976
-
-
Qing, K.1
Hansen, J.2
Weigel-Kelley, K.A.3
-
46
-
-
0019859168
-
A cascade of adenovirus early functions is required for expression of adeno-associated virus
-
Richardson, W.D. and Westphal, H. A cascade of adenovirus early functions is required for expression of adeno-associated virus. Cell 1981, 27: 133-41.
-
(1981)
Cell
, vol.27
, pp. 133-141
-
-
Richardson, W.D.1
Westphal, H.2
-
47
-
-
0038150506
-
Helper virus-free, optically controllable, and two-plasmid-based production of adeno-associated virus vectors of serotypes 1 to 6
-
Grimm, D., Kay, M.A. and Kleinschmidt, J.A. Helper virus-free, optically controllable, and two-plasmid-based production of adeno-associated virus vectors of serotypes 1 to 6. Mol Ther 2003, 7: 839-50.
-
(2003)
Mol Ther
, vol.7
, pp. 839-850
-
-
Grimm, D.1
Kay, M.A.2
Kleinschmidt, J.A.3
-
48
-
-
4043167741
-
The adenovirus E1A and E1B19K genes provide a helper function for transfection-based adeno-associated virus production
-
Matsushita, T., Okada, T., Inaba, T. et al. The adenovirus E1A and E1B19K genes provide a helper function for transfection-based adeno-associated virus production. J Gen Virol 2004, 85: 2209-14.
-
(2004)
J Gen Virol
, vol.85
, pp. 2209-2214
-
-
Matsushita, T.1
Okada, T.2
Inaba, T.3
-
49
-
-
4644346385
-
Improving rAAV production and purification: Towards the definition of a scaleable process
-
Blouin, V., Brument, N., Toublanc, E. et al. Improving rAAV production and purification: Towards the definition of a scaleable process. J Gene Med 2004, 6: S223-8.
-
(2004)
J Gene Med
, vol.6
-
-
Blouin, V.1
Brument, N.2
Toublanc, E.3
-
50
-
-
0242643501
-
Serum-free production and column purification of adeno-associated virus type 5
-
Smith, R.H., Ding, C. and Kotin, R.M. Serum-free production and column purification of adeno-associated virus type 5. J Virol Methods 2003, 114: 115-24.
-
(2003)
J Virol Methods
, vol.114
, pp. 115-124
-
-
Smith, R.H.1
Ding, C.2
Kotin, R.M.3
-
51
-
-
0032917854
-
Viral receptors and vector purification: New approaches for generating clinical-grade reagents
-
Summerford, C. and Samulski, R.J. Viral receptors and vector purification: New approaches for generating clinical-grade reagents. Nat Med 1999, 5: 587-8.
-
(1999)
Nat Med
, vol.5
, pp. 587-588
-
-
Summerford, C.1
Samulski, R.J.2
-
52
-
-
0036140216
-
Cross-packaging of a single adeno-associated virus (AAV) type 2 vector genome into multiple AAV serotypes enables transduction with broad specificity
-
Rabinowitz, J.E., Rolling, F., Li, C. et al. Cross-packaging of a single adeno-associated virus (AAV) type 2 vector genome into multiple AAV serotypes enables transduction with broad specificity. J Virol 2002, 76: 791-801.
-
(2002)
J Virol
, vol.76
, pp. 791-801
-
-
Rabinowitz, J.E.1
Rolling, F.2
Li, C.3
-
53
-
-
4444352441
-
Cross-dressing the virion: The transcapsidation of adeno-associated virus serotypes functionally defines subgroups
-
Rabinowitz, J.E., Boules, D.E., Faust, S.M. et al. Cross-dressing the virion: The transcapsidation of adeno-associated virus serotypes functionally defines subgroups. J Virol 2004, 78: 4421-32.
-
(2004)
J Virol
, vol.78
, pp. 4421-4432
-
-
Rabinowitz, J.E.1
Boules, D.E.2
Faust, S.M.3
-
54
-
-
0034724209
-
Recombinant adeno-associated virus type 2, 4, and 5 vectors: Transduction of variant cell types and regions in the mammalian central nervous system
-
Davidson, B.L., Stein, C.S., Heth, J.A. et al. Recombinant adeno-associated virus type 2, 4, and 5 vectors: Transduction of variant cell types and regions in the mammalian central nervous system. Proc Natl Acad Sci USA 2000, 97: 3428-32.
-
(2000)
Proc Natl Acad Sci USA
, vol.97
, pp. 3428-3432
-
-
Davidson, B.L.1
Stein, C.S.2
Heth, J.A.3
-
55
-
-
0041808929
-
Receptor targeting of adeno-associated virus vectors
-
Buning, H., Ried, M.U., Perabo, L. et al. Receptor targeting of adeno-associated virus vectors. Gene Ther 2003, 10: 1142-51.
-
(2003)
Gene Ther
, vol.10
, pp. 1142-1151
-
-
Buning, H.1
Ried, M.U.2
Perabo, L.3
-
56
-
-
0041375553
-
Targeting recombinant adeno-associated virus vectors to enhance gene transfer to pancreatic islets and liver
-
Loiler, S.A., Conlon, T.J., Song, S. et al. Targeting recombinant adeno-associated virus vectors to enhance gene transfer to pancreatic islets and liver. Gene Ther 2003, 10: 1551-8.
-
(2003)
Gene Ther
, vol.10
, pp. 1551-1558
-
-
Loiler, S.A.1
Conlon, T.J.2
Song, S.3
-
57
-
-
0033851104
-
Mutational analysis of the adeno-associated virus type 2 (AAV2) capsid gene and construction of AAV2 vectors with altered tropism
-
Wu, P., Xiao, W., Conlon, T. et al. Mutational analysis of the adeno-associated virus type 2 (AAV2) capsid gene and construction of AAV2 vectors with altered tropism. J Virol 2000, 74: 8635-47.
-
(2000)
J Virol
, vol.74
, pp. 8635-8647
-
-
Wu, P.1
Xiao, W.2
Conlon, T.3
-
58
-
-
2642537522
-
Circulating anti-wild-type adeno-associated virus type 2 (AAV2) antibodies inhibit recombinant AAV2 (rAAV2)-mediated, but not rAAV5-mediated, gene transfer in the brain
-
Peden, C.S., Burger, C., Muzyczka, N. and Mandel, R.J. Circulating anti-wild-type adeno-associated virus type 2 (AAV2) antibodies inhibit recombinant AAV2 (rAAV2)-mediated, but not rAAV5-mediated, gene transfer in the brain. J Virol 2004, 78: 6344-59.
-
(2004)
J Virol
, vol.78
, pp. 6344-6359
-
-
Peden, C.S.1
Burger, C.2
Muzyczka, N.3
Mandel, R.J.4
-
59
-
-
0015144322
-
A seroepidemiologic study of adenovirus-associated virus infection in infants and children
-
Blacklow, N.R., Hoggan, M.D., Sereno, M.S. et al. A seroepidemiologic study of adenovirus-associated virus infection in infants and children. Am J Epidemiol 1971, 94: 359-66.
-
(1971)
Am J Epidemiol
, vol.94
, pp. 359-366
-
-
Blacklow, N.R.1
Hoggan, M.D.2
Sereno, M.S.3
-
60
-
-
0032853699
-
Immune responses to adenovirus and adeno-associated virus in humans
-
Chirmule, N., Propert, K., Magosin, S. et al. Immune responses to adenovirus and adeno-associated virus in humans. Gene Ther 1999, 6: 1574-83.
-
(1999)
Gene Ther
, vol.6
, pp. 1574-1583
-
-
Chirmule, N.1
Propert, K.2
Magosin, S.3
-
61
-
-
0345411588
-
Update on the prevalence of serum antibodies (IgG and IgM) to adeno-associated virus (AAV)
-
Erles, K., Sebokova, P. and Schlehofer, J.R. Update on the prevalence of serum antibodies (IgG and IgM) to adeno-associated virus (AAV). J Med Virol 1999, 59: 406-11.
-
(1999)
J Med Virol
, vol.59
, pp. 406-411
-
-
Erles, K.1
Sebokova, P.2
Schlehofer, J.R.3
-
62
-
-
0021340974
-
Analysis of proteins, helper dependence, and seroepidemiology of a new human parvovirus
-
Georg-Fries, B., Biederlack, S., Wolf, J. and zur Hausen, H. Analysis of proteins, helper dependence, and seroepidemiology of a new human parvovirus. Virology 1984, 134: 64-71.
-
(1984)
Virology
, vol.134
, pp. 64-71
-
-
Georg-Fries, B.1
Biederlack, S.2
Wolf, J.3
Zur Hausen, H.4
-
63
-
-
0034882826
-
Self-inactivating recombinant adeno-associated virus (scAAV) vectors promote efficient transduction independently of DNA synthesis
-
McCarty, D.M., Monahan, P.E. and Samulski, R.J. Self-inactivating recombinant adeno-associated virus (scAAV) vectors promote efficient transduction independently of DNA synthesis. Gene Ther 2001, 8: 1248-54.
-
(2001)
Gene Ther
, vol.8
, pp. 1248-1254
-
-
McCarty, D.M.1
Monahan, P.E.2
Samulski, R.J.3
-
64
-
-
0036127393
-
Modular flexibility of dystrophin: Implications for gene therapy of Duchenne muscular dystrophy
-
Harper, S.Q., Hauser, M.A., Dellorusso, C. et al. Modular flexibility of dystrophin: Implications for gene therapy of Duchenne muscular dystrophy. Nat Med 2002, 8: 253-61.
-
(2002)
Nat Med
, vol.8
, pp. 253-261
-
-
Harper, S.Q.1
Hauser, M.A.2
Dellorusso, C.3
-
65
-
-
0034121397
-
A new dual-vector approach to enhance recombinant adeno-associated virus-mediated gene expression through intermolecular cis activation
-
Duan, D., Yue, Y., Yan, Z. et al. A new dual-vector approach to enhance recombinant adeno-associated virus-mediated gene expression through intermolecular cis activation. Nat Med 2000, 6: 595-8.
-
(2000)
Nat Med
, vol.6
, pp. 595-598
-
-
Duan, D.1
Yue, Y.2
Yan, Z.3
-
66
-
-
0034033447
-
Increasing the size of rAAV-mediated expression cassettes in vivo by intermolecular joining of two complementary vectors
-
Nakai, H., Storm, T.A. and Kay, M.A. Increasing the size of rAAV-mediated expression cassettes in vivo by intermolecular joining of two complementary vectors. Nat Biotechnol 2000, 18: 527-32.
-
(2000)
Nat Biotechnol
, vol.18
, pp. 527-532
-
-
Nakai, H.1
Storm, T.A.2
Kay, M.A.3
-
67
-
-
0034121579
-
Overcoming adeno-associated virus vector size limitation through viral DNA heterodimerization
-
Sun, L., Li, J. and Xiao, X. Overcoming adeno-associated virus vector size limitation through viral DNA heterodimerization. Nat Med 2000, 6: 599-602.
-
(2000)
Nat Med
, vol.6
, pp. 599-602
-
-
Sun, L.1
Li, J.2
Xiao, X.3
-
68
-
-
0037461732
-
Second cancer case halts gene-therapy trials
-
Check, E. Second cancer case halts gene-therapy trials. Nature 2003, 421: 305.
-
(2003)
Nature
, vol.421
, pp. 305
-
-
Check, E.1
-
69
-
-
1342289322
-
Activation of the T-cell oncogene LMO2 after gene therapy for X-linked severe combined immunodeficiency
-
McCormack, M.P. and Rabbitts, T.H. Activation of the T-cell oncogene LMO2 after gene therapy for X-linked severe combined immunodeficiency. N Engl J Med 2004, 350: 913-22.
-
(2004)
N Engl J Med
, vol.350
, pp. 913-922
-
-
McCormack, M.P.1
Rabbitts, T.H.2
-
70
-
-
0028307303
-
Adeno-associated virus (AAV) Rep proteins mediate complex formation between AAV DNA and its integration site in human DNA
-
Weitzman, M.D., Kyostio, S.R., Kotin, R.M. et al. Adeno-associated virus (AAV) Rep proteins mediate complex formation between AAV DNA and its integration site in human DNA. Proc Natl Acad Sci USA 1994, 91: 5808-12.
-
(1994)
Proc Natl Acad Sci USA
, vol.91
, pp. 5808-5812
-
-
Weitzman, M.D.1
Kyostio, S.R.2
Kotin, R.M.3
-
71
-
-
0034830365
-
Observed incidence of tumorigenesis in long-term rodent studies of rAAV vectors
-
Donsante, A., Vogler, C., Muzyczka, N. et al. Observed incidence of tumorigenesis in long-term rodent studies of rAAV vectors. Gene Ther 2001, 8: 1343-6.
-
(2001)
Gene Ther
, vol.8
, pp. 1343-1346
-
-
Donsante, A.1
Vogler, C.2
Muzyczka, N.3
-
72
-
-
0036478954
-
Chromosomal effects of adeno-associated virus vector integration
-
Miller, D.G., Rutledge, E.A. and Russell, D.W. Chromosomal effects of adeno-associated virus vector integration. Nat Genet 2002, 30: 147-8.
-
(2002)
Nat Genet
, vol.30
, pp. 147-148
-
-
Miller, D.G.1
Rutledge, E.A.2
Russell, D.W.3
-
73
-
-
0038054338
-
AAV serotype 2 vectors preferentially integrate into active genes in mice
-
Nakai, H., Montini, E., Fuess, S. et al. AAV serotype 2 vectors preferentially integrate into active genes in mice. Nat Genet 2003, 34: 297-302.
-
(2003)
Nat Genet
, vol.34
, pp. 297-302
-
-
Nakai, H.1
Montini, E.2
Fuess, S.3
-
74
-
-
0030693895
-
Oncogenes and antioncogenes involved in human thyroid carcinogenesis
-
Lazzareschi, D., Mincione, G., Coppa, A. et al. Oncogenes and antioncogenes involved in human thyroid carcinogenesis. J Exp Clin Canc Res 1997, 16: 325-32.
-
(1997)
J Exp Clin Canc Res
, vol.16
, pp. 325-332
-
-
Lazzareschi, D.1
Mincione, G.2
Coppa, A.3
-
75
-
-
1242269713
-
How does a normal cell become a cancer cell?
-
Gan, D.D., Macaluso, M., Cinti, C. et al. How does a normal cell become a cancer cell? J Exp Clin Cane Res 2003, 22: 509-16.
-
(2003)
J Exp Clin Cane Res
, vol.22
, pp. 509-516
-
-
Gan, D.D.1
Macaluso, M.2
Cinti, C.3
|