메뉴 건너뛰기




Volumn 10, Issue 18, 2003, Pages 1551-1558

Targeting recombinant adeno-associated virus vectors to enhance gene transfer to pancreatic islets and liver

Author keywords

Adeno associated virus; Diabetes; Targeting

Indexed keywords

APOLIPOPROTEIN; LIGAND; LOW DENSITY LIPOPROTEIN RECEPTOR; PARVOVIRUS VECTOR; VIRUS VECTOR;

EID: 0041375553     PISSN: 09697128     EISSN: None     Source Type: Journal    
DOI: 10.1038/sj.gt.3302046     Document Type: Article
Times cited : (99)

References (34)
  • 1
    • 0035928391 scopus 로고    scopus 로고
    • Type 1 diabetes: New perspectives on disease pathogenesis and treatment
    • Atkinson MA, Eisenbarth GS. Type 1 diabetes: new perspectives on disease pathogenesis and treatment. Lancet 2001; 358: 221-229.
    • (2001) Lancet , vol.358 , pp. 221-229
    • Atkinson, M.A.1    Eisenbarth, G.S.2
  • 2
    • 0028966354 scopus 로고
    • Long-term (> 3-year) insulin independence in a patient with pancreatic islet cell transplantation following upper abdominal exenteration and liver replacement for fibrolamellar hepatocellular carcinoma
    • Carroll PB et al. Long-term (> 3-year) insulin independence in a patient with pancreatic islet cell transplantation following upper abdominal exenteration and liver replacement for fibrolamellar hepatocellular carcinoma. Transplantation 1995; 59: 875-879.
    • (1995) Transplantation , vol.59 , pp. 875-879
    • Carroll, P.B.1
  • 3
    • 0032462398 scopus 로고    scopus 로고
    • Islet transplantation: Present and future perspectives
    • Kenyon N et al. Islet transplantation: present and future perspectives. Diabetes Metab Rev 1998; 14: 303-313.
    • (1998) Diabetes Metab. Rev. , vol.14 , pp. 303-313
    • Kenyon, N.1
  • 4
    • 0033842203 scopus 로고    scopus 로고
    • Islet cell transplantation: In vivo and in vitro functional assessment of nonhuman primate pancreatic islets
    • Ranuncoli A et al. Islet cell transplantation: in vivo and in vitro functional assessment of nonhuman primate pancreatic islets. Cell Transplant 2000; 9: 409-414.
    • (2000) Cell Transplant. , vol.9 , pp. 409-414
    • Ranuncoli, A.1
  • 5
    • 0034721255 scopus 로고    scopus 로고
    • Islet transplantation in seven patients with type 1 diabetes mellitus using a glucocorticoid-free immunosuppressive regimen
    • Shapiro AM et al. Islet transplantation in seven patients with type 1 diabetes mellitus using a glucocorticoid-free immunosuppressive regimen. N Engl J Med 2000; 343: 230-238.
    • (2000) N. Engl. J. Med. , vol.343 , pp. 230-238
    • Shapiro, A.M.1
  • 6
    • 0027064638 scopus 로고
    • Islet cell transplantation facilitated by gene transfer
    • Tahara H et al. Islet cell transplantation facilitated by gene transfer. Transplant Proc 1992; 24: 2975-2976.
    • (1992) Transplant. Proc. , vol.24 , pp. 2975-2976
    • Tahara, H.1
  • 7
    • 0035127574 scopus 로고    scopus 로고
    • Efficient ex vivo transduction of pancreatic islet cells with recombinant adeno-associated virus vectors
    • Flotte T et al. Efficient ex vivo transduction of pancreatic islet cells with recombinant adeno-associated virus vectors. Diabetes 2001; 50: 515-520.
    • (2001) Diabetes , vol.50 , pp. 515-520
    • Flotte, T.1
  • 8
    • 0034635155 scopus 로고    scopus 로고
    • The receptor binding domain of apolipoprotein E, linked to a model class A amphipathic helix, enhances internalization and degradation of LDL by fibroblasts
    • Datta G et al. The receptor binding domain of apolipoprotein E, linked to a model class A amphipathic helix, enhances internalization and degradation of LDL by fibroblasts. Biochemistry 2000; 39: 213-220.
    • (2000) Biochemistry , vol.39 , pp. 213-220
    • Datta, G.1
  • 9
    • 0031906147 scopus 로고    scopus 로고
    • Membrane-associated heparan sulfate proteoglycan is a receptor for adeno-associated virus type 2 virions
    • Summerford C, Samulski RJ. Membrane-associated heparan sulfate proteoglycan is a receptor for adeno-associated virus type 2 virions. J Virol 1998; 72: 1438-1445.
    • (1998) J. Virol. , vol.72 , pp. 1438-1445
    • Summerford, C.1    Samulski, R.J.2
  • 10
    • 0034957168 scopus 로고    scopus 로고
    • Adeno-associated virus serotype 4 (AAV4) and AAV5 both require sialic acid binding for hemagglutination and efficient transduction but differ in sialic acid linkage specificity
    • Kaludov N et al. Adeno-associated virus serotype 4 (AAV4) and AAV5 both require sialic acid binding for hemagglutination and efficient transduction but differ in sialic acid linkage specificity. J Virol 2001; 75: 6884-6893.
    • (2001) J. Virol. , vol.75 , pp. 6884-6893
    • Kaludov, N.1
  • 11
    • 0034766041 scopus 로고    scopus 로고
    • A single-step affinity column for purification of serotype-5 based adeno-associated viral vectors
    • Auricchio A, O'Connor E, Hildinger M, Wilson JM. A single-step affinity column for purification of serotype-5 based adeno-associated viral vectors. Mol Ther 2001; 4: 372-374.
    • (2001) Mol. Ther. , vol.4 , pp. 372-374
    • Auricchio, A.1    O'Connor, E.2    Hildinger, M.3    Wilson, J.M.4
  • 12
    • 0035827546 scopus 로고    scopus 로고
    • Binding of adeno-associated virus type 5 to 2,3-linked sialic acid is required for gene transfer
    • Walters RW et al. Binding of adeno-associated virus type 5 to 2,3-linked sialic acid is required for gene transfer. J Biol Chem 2001; 276: 20610-20616.
    • (2001) J. Biol. Chem. , vol.276 , pp. 20610-20616
    • Walters, R.W.1
  • 13
    • 0036174267 scopus 로고    scopus 로고
    • Endocytosis of adeno-associated virus type 5 leads to accumulation of virus particles in the Golgi compartment
    • Bantel-Schaal U, Hub B, Kartenbeck J. Endocytosis of adeno-associated virus type 5 leads to accumulation of virus particles in the Golgi compartment. J Virol 2002; 76: 2340-2349.
    • (2002) J. Virol. , vol.76 , pp. 2340-2349
    • Bantel-Schaal, U.1    Hub, B.2    Kartenbeck, J.3
  • 14
    • 0035401103 scopus 로고    scopus 로고
    • Rate limiting steps of AAV transduction and implications for human gene therapy
    • Sanlioglu S et al. Rate limiting steps of AAV transduction and implications for human gene therapy. Curr Gene Ther 2001; 1: 137-147.
    • (2001) Curr. Gene Ther. , vol.1 , pp. 137-147
    • Sanlioglu, S.1
  • 15
    • 0036140216 scopus 로고    scopus 로고
    • Cross-packaging of a single adeno-associated virus (AAV) type 2 vector genome into multiple AAV serotypes enables transduction with broad specificity
    • Rabinowitz JE et al. Cross-packaging of a single adeno-associated virus (AAV) type 2 vector genome into multiple AAV serotypes enables transduction with broad specificity. J Virol 2002; 76: 791-801.
    • (2002) J. Virol. , vol.76 , pp. 791-801
    • Rabinowitz, J.E.1
  • 16
    • 0033851104 scopus 로고    scopus 로고
    • Mutational analysis of the adeno-associated virus type 2 (AAV2) capsid gene and construction of AAV2 vectors with altered tropism
    • [In Process Citation]
    • Wu P et al. Mutational analysis of the adeno-associated virus type 2 (AAV2) capsid gene and construction of AAV2 vectors with altered tropism [In Process Citation]. J Virol 2000; 74: 8635-8647.
    • (2000) J. Virol. , vol.74 , pp. 8635-8647
    • Wu, P.1
  • 17
    • 0035196616 scopus 로고    scopus 로고
    • The LDL receptor is the major pathway for beta-VLDL uptake by mouse peritoneal macrophages
    • Perrey S et al. The LDL receptor is the major pathway for beta-VLDL uptake by mouse peritoneal macrophages. Atherosclerosis 2001; 154: 51-60.
    • (2001) Atherosclerosis , vol.154 , pp. 51-60
    • Perrey, S.1
  • 18
    • 0029880461 scopus 로고    scopus 로고
    • Interaction of a recombinant form of apolipoprotein[a] with human fibroblasts and with the human hepatoma cell line HepG2
    • Tam SP, Zhang X, Koschinsky ML. Interaction of a recombinant form of apolipoprotein[a] with human fibroblasts and with the human hepatoma cell line HepG2. J Lipid Res 1996; 37: 518-533.
    • (1996) J. Lipid. Res. , vol.37 , pp. 518-533
    • Tam, S.P.1    Zhang, X.2    Koschinsky, M.L.3
  • 19
    • 0035652754 scopus 로고    scopus 로고
    • Dynamic and stable pools of apoE differ functionally at the HepG2 cell surface
    • Burgess JW, Marcel YL. Dynamic and stable pools of apoE differ functionally at the HepG2 cell surface. J Lipid Res 2001; 42: 1413-1420.
    • (2001) J. Lipid Res. , vol.42 , pp. 1413-1420
    • Burgess, J.W.1    Marcel, Y.L.2
  • 20
    • 0033007934 scopus 로고    scopus 로고
    • Targeted adeno-associated virus vector transduction of nonpermissive cells mediated by a bispecific F(ab'gamma)2 antibody
    • Bartlett JS, Kleinschmidt J, Boucher RC, Samulski RJ. Targeted adeno-associated virus vector transduction of nonpermissive cells mediated by a bispecific F(ab'gamma)2 antibody. Nat Biotechnol 1999; 17: 181-186.
    • (1999) Nat. Biotechnol. , vol.17 , pp. 181-186
    • Bartlett, J.S.1    Kleinschmidt, J.2    Boucher, R.C.3    Samulski, R.J.4
  • 21
    • 0034963928 scopus 로고    scopus 로고
    • Incorporation of tumor-targeting peptides into recombinant adeno-associated virus capsids
    • Grifman M et al. Incorporation of tumor-targeting peptides into recombinant adeno-associated virus capsids. Mol Ther 2001; 3: 964-975.
    • (2001) Mol. Ther. , vol.3 , pp. 964-975
    • Grifman, M.1
  • 22
    • 0034843445 scopus 로고    scopus 로고
    • Efficient and selective AAV2-mediated gene transfer directed to human vascular endothelial cells
    • Nicklin SA et al. Efficient and selective AAV2-mediated gene transfer directed to human vascular endothelial cells. Mol Ther 2001; 4: 174-181.
    • (2001) Mol. Ther. , vol.4 , pp. 174-181
    • Nicklin, S.A.1
  • 23
    • 0034814413 scopus 로고    scopus 로고
    • Insertional mutagenesis of the adeno-associated virus type 2 (AAV2) capsid gene and generation of AAV2 vectors targeted to alternative cell-surface receptors
    • Shi W, Arnold GS, Bartlett JS. Insertional mutagenesis of the adeno-associated virus type 2 (AAV2) capsid gene and generation of AAV2 vectors targeted to alternative cell-surface receptors. Hum Gene Ther 2001; 12: 1697-1711.
    • (2001) Hum. Gene Ther. , vol.12 , pp. 1697-1711
    • Shi, W.1    Arnold, G.S.2    Bartlett, J.S.3
  • 24
    • 0032170198 scopus 로고    scopus 로고
    • Development of novel cell surface CD34-targeted recombinant adenoassociated virus vectors for gene therapy
    • Yang Q et al. Development of novel cell surface CD34-targeted recombinant adenoassociated virus vectors for gene therapy. Hum Gene Ther 1998; 9: 1929-1937.
    • (1998) Hum. Gene Ther. , vol.9 , pp. 1929-1937
    • Yang, Q.1
  • 25
    • 0033766932 scopus 로고    scopus 로고
    • Glucose-responsive gene delivery in pancreatic Islet cells via recombinant adeno-associated viral vectors
    • Yang YW, Kotin RM. Glucose-responsive gene delivery in pancreatic Islet cells via recombinant adeno-associated viral vectors. Pharm Res 2000; 17: 1056-61.
    • (2000) Pharm. Res. , vol.17 , pp. 1056-1061
    • Yang, Y.W.1    Kotin, R.M.2
  • 26
    • 0036277129 scopus 로고    scopus 로고
    • Mechanisms that regulate silencing of gene expression from retroviral vectors
    • Swindle CS, Klug CA. Mechanisms that regulate silencing of gene expression from retroviral vectors. J Hematother Stem Cell Res 2002; 11: 449-456.
    • (2002) J. Hematother. Stem Cell Res. , vol.11 , pp. 449-456
    • Swindle, C.S.1    Klug, C.A.2
  • 27
    • 0036714352 scopus 로고    scopus 로고
    • Modification of multiple transcriptional regulatory elements in a Moloney murine leukemia virus gene transfer vector circumvents silencing in fibroblast grafts and increases levels of expression of the transferred enzyme
    • Prasad Alur RK et al. Modification of multiple transcriptional regulatory elements in a Moloney murine leukemia virus gene transfer vector circumvents silencing in fibroblast grafts and increases levels of expression of the transferred enzyme. Gene Therapy 2002; 9: 1645.
    • (2002) Gene Therapy , vol.9 , pp. 1645
    • Prasad Alur, R.K.1
  • 28
    • 0032506750 scopus 로고    scopus 로고
    • Lentivirus-mediated transduction of islet grafts with interleukin 4 results in sustained gene expression and protection from insulitis
    • Gallichan WS et al. Lentivirus-mediated transduction of islet grafts with interleukin 4 results in sustained gene expression and protection from insulitis. Hum Gene Ther 1998; 9: 2717-2726.
    • (1998) Hum. Gene. Ther. , vol.9 , pp. 2717-2726
    • Gallichan, W.S.1
  • 29
    • 0029838995 scopus 로고    scopus 로고
    • Pancreatic expression of interleukin-4 abrogates insulitis and autoimmune diabetes in nonobese diabetic (NOD) mice
    • Mueller R, Krahl T, Sarvetnick N. Pancreatic expression of interleukin-4 abrogates insulitis and autoimmune diabetes in nonobese diabetic (NOD) mice. J Exp Med 1996; 184: 1093-1099.
    • (1996) J. Exp. Med. , vol.184 , pp. 1093-1099
    • Mueller, R.1    Krahl, T.2    Sarvetnick, N.3
  • 30
    • 0035458338 scopus 로고    scopus 로고
    • Heme oxygenase-1 induction in islet cells results in protection from apoptosis and improved in vivo function after transplantation
    • Pileggi A et al. Heme oxygenase-1 induction in islet cells results in protection from apoptosis and improved in vivo function after transplantation. Diabetes 2001; 50: 1983-1991.
    • (2001) Diabetes , vol.50 , pp. 1983-1991
    • Pileggi, A.1
  • 31
    • 0035937316 scopus 로고    scopus 로고
    • CMV-beta-actin promoter directs higher expression from an adeno- associated viral vector in the liver than the cytomegalovirus or elongation factor 1 alpha promoter and results in therapeutic levels of human factor X in mice
    • Xu L et al. CMV-beta-actin promoter directs higher expression from an adeno- associated viral vector in the liver than the cytomegalovirus or elongation factor 1 alpha promoter and results in therapeutic levels of human factor X in mice. Hum Gene Ther 2001; 12: 563-573.
    • (2001) Hum. Gene Ther. , vol.12 , pp. 563-573
    • Xu, L.1
  • 32
    • 0025946426 scopus 로고
    • Sequences required for coordinate induction of adeno-associated virus p19 and p40 promoters by Rep protein
    • McCarty DM, Christensen M, Muzyczka N. Sequences required for coordinate induction of adeno-associated virus p19 and p40 promoters by Rep protein. J Virol 1991; 65: 2936-2945.
    • (1991) J. Virol. , vol.65 , pp. 2936-2945
    • McCarty, D.M.1    Christensen, M.2    Muzyczka, N.3
  • 33
    • 0033022953 scopus 로고    scopus 로고
    • Recombinant adeno-associated virus purification using novel methods improves infectious titer and yield
    • Zolotukhin S et al. Recombinant adeno-associated virus purification using novel methods improves infectious titer and yield. Gene Therapy 1999; 6: 973-985.
    • (1999) Gene Therapy , vol.6 , pp. 973-985
    • Zolotukhin, S.1
  • 34
    • 2642642141 scopus 로고    scopus 로고
    • Production of high-titer recombinant adeno-associated virus vectors in the absence of helper adenovirus
    • Xiao X, Li J, Samulski RJ. Production of high-titer recombinant adeno-associated virus vectors in the absence of helper adenovirus. J Virol 1998; 72: 2224-2232.
    • (1998) J. Virol. , vol.72 , pp. 2224-2232
    • Xiao, X.1    Li, J.2    Samulski, R.J.3


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.