Long-term enzyme correction and lipid reduction in multiple organs of primary and secondary transplanted Fabry mice receiving transduced bone marrow cells

Proceedings of the National Academy of Sciences of the United States of America

Volumn 97, Issue 13, 2000, Pages 7515-7520

  Takenaka, Toshihiro ^a,d   Murray, Gary J ^a   Qin, Gangjian ^c   Quirk, Jane M ^a   Ohshima, Toshio ^b   Qasba, Pankaj ^a   Clark, Kelly ^c   Kulkarni, Ashok B ^b   Brady, Roscoe O ^a   Medin, Jeffrey A ^c  

^a NATIONAL INSTITUTE OF NEUROLOGICAL DISORDERS AND STROKE   (United States)

^b NATIONAL INSTITUTE OF DENTAL AND CRANIOFACIAL RESEARCH   (United States)

^c UNIVERSITY OF ILLINOIS AT CHICAGO   (United States)

^d KAGOSHIMA UNIVERSITY   (Japan)

Author keywords

[No Author keywords available]

Indexed keywords

ALPHA GALACTOSIDASE;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; BLOOD VESSEL OCCLUSION; BONE MARROW CELL; BONE MARROW TRANSPLANTATION; CONTROLLED STUDY; ENDOCYTOSIS; ENZYME DEFECT; FABRY DISEASE; GENE OVEREXPRESSION; GENE THERAPY; GENETIC TRANSDUCTION; MALE; MOUSE; NONHUMAN; PRIORITY JOURNAL; RETROVIRUS;

ALPHA-GALACTOSIDASE; ANIMALS; BONE MARROW CELLS; BONE MARROW TRANSPLANTATION; FABRY DISEASE; GENE EXPRESSION; GENE TRANSFER TECHNIQUES; LIPID METABOLISM; MICE; MICE, KNOCKOUT; ORGAN SPECIFICITY; TIME FACTORS;

EID: 12944269059     PISSN: 00278424     EISSN: None     Source Type: Journal    
DOI: 10.1073/pnas.120177997     Document Type: Article

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