Correction in trans for Fabry disease: Expression, secretion, and uptake of a-galactosidase A in patient-derived cells driven by a high-titer recombinant retroviral vector

Proceedings of the National Academy of Sciences of the United States of America

Volumn 93, Issue 15, 1996, Pages 7917-7922

  Medin, Jeffrey A ^a,b   Tudor, Matthew ^a   Simovitch, Ryan ^a   Quirk, Jane M ^a   Jacobson, Steven ^a   Murray, Gary J ^a   Brady, Roscoe O ^a  

^a NATIONAL INSTITUTE OF NEUROLOGICAL DISORDERS AND STROKE   (United States)

^b NATIONAL INSTITUTES OF HEALTH   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ALPHA GALACTOSIDASE; VIRUS VECTOR;

ANIMAL CELL; ARTICLE; CELL CULTURE; ENZYME ACTIVITY; ENZYME ANALYSIS; ENZYME DEFECT; ENZYME DEFICIENCY; FABRY DISEASE; GENE EXPRESSION; GENE TRANSFER; NONHUMAN; PRIORITY JOURNAL; TARGET CELL;

3T3 CELLS; ALPHA-GALACTOSIDASE; ANIMALS; B-LYMPHOCYTES; BASE SEQUENCE; CELL LINE; CELLS, CULTURED; DNA PRIMERS; FABRY DISEASE; FIBROBLASTS; GENE THERAPY; GENETIC VECTORS; HUMANS; LEUKOCYTES; MICE; MOLECULAR SEQUENCE DATA; POLYMERASE CHAIN REACTION; RETROVIRIDAE; SKIN; TRANSFECTION; X CHROMOSOME;

ANIMALIA; UNIDENTIFIED RETROVIRUS;

EID: 0029836764     PISSN: 00278424     EISSN: None     Source Type: Journal    
DOI: 10.1073/pnas.93.15.7917     Document Type: Article

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