Gene transfer and expression of human α-galactosidase from mouse muscle in vitro and in vivo

Gene Therapy

Volumn 4, Issue 5, 1997, Pages 488-492

  Novo, F J ^a,b   Gorecki D C ^a   Goldspink, G ^a   MacDermot, K D ^a  

^a ROYAL FREE HOSPITAL   (United Kingdom)

^b UNIVERSITY OF NAVARRA   (Spain)

Author keywords

Direct muscle injection; Muscle expression vectors; gal

Indexed keywords

ALPHA GALACTOSIDASE; CELL EXTRACT; MANNOSE 6 PHOSPHATE; MYOSIN HEAVY CHAIN; MYOSIN LIGHT CHAIN; SOMATOMEDIN B RECEPTOR;

ANIMAL CELL; ANIMAL EXPERIMENT; ARTICLE; CELL DIFFERENTIATION; CELL LINE; CONTROLLED STUDY; ENHANCER REGION; ENZYME ACTIVITY; ENZYME RELEASE; EXPRESSION VECTOR; FIBROBLAST; GENE CONSTRUCT; GENE TRANSFER; GENETICS; HUMAN CYTOMEGALOVIRUS; LYSOSOME STORAGE DISEASE; MOUSE; MYOTUBE; NONHUMAN; PLASMID; PRIORITY JOURNAL; PROMOTER REGION; RABBIT; SKELETAL MUSCLE; SUPERNATANT; TIBIALIS ANTERIOR MUSCLE;

ANIMALIA; CUCUMBER MOSAIC VIRUS; HUMAN HERPESVIRUS 5; ORYCTOLAGUS CUNICULUS;

EID: 0030914425     PISSN: 09697128     EISSN: None     Source Type: Journal    
DOI: 10.1038/sj.gt.3300410     Document Type: Article

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