Upregulation of expression from the FRDA genomic locus for the therapy of Friedreich ataxia

Journal of Gene Medicine

Volumn 5, Issue 1, 2003, Pages 72-81

  Sarsero, Joseph P ^a   Li, Lingli ^a   Wardan, Hady ^a   Sitte, Karin ^a   Williamson, Robert ^a   Ioannou, Panos A ^a  

^a ROYAL CHILDREN'S HOSPITAL   (Australia)

Author keywords

BAC; EGFP; Frataxin; FRDA; Friedreich ataxia; Homologous recombination

Indexed keywords

BUTYRIC ACID; ENHANCED GREEN FLUORESCENT PROTEIN; FRATAXIN; HEMIN; HYBRID PROTEIN; KANAMYCIN; MESSENGER RNA; NEOMYCIN; IRON BINDING PROTEIN;

ANTIBIOTIC RESISTANCE; ARTICLE; BACTERIAL ARTIFICIAL CHROMOSOME; CELL LINE; EXON; FRIEDREICH ATAXIA; GENE CASSETTE; GENE CONSTRUCT; GENE EXPRESSION; GENE EXPRESSION REGULATION; GENE FUSION; GENE IDENTIFICATION; GENE INSERTION; GENE LOCUS; GENE SEQUENCE; GENE TARGETING; GENETIC ENGINEERING; GENETIC SCREENING; HOMOLOGOUS RECOMBINATION; HUMAN; MITOCHONDRION; MOLECULAR CLONING; NUCLEOTIDE SEQUENCE; PRIORITY JOURNAL; REGULATORY SEQUENCE; UPREGULATION; BACTERIOPHAGE P1 ARTIFICIAL CHROMOSOME; GENE TRANSFER; GENETICS; METABOLISM; PHYSIOLOGY; REPORTER GENE;

CHROMOSOMES, ARTIFICIAL, BACTERIAL; CHROMOSOMES, ARTIFICIAL, P1 BACTERIOPHAGE; FRIEDREICH ATAXIA; GENE EXPRESSION REGULATION; GENE TRANSFER TECHNIQUES; GENES, REPORTER; HUMANS; IRON-BINDING PROTEINS; RECOMBINANT FUSION PROTEINS; UP-REGULATION;

EID: 0038448961     PISSN: 1099498X     EISSN: None     Source Type: Journal    
DOI: 10.1002/jgm.320     Document Type: Article

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