Hematopoietic stem cell gene therapy for inherited bone marrow disorders: Past accomplishments and continued challenges

Journal of Cellular Biochemistry

Volumn 85, Issue SUPPL. 38, 2002, Pages 55-64

  Yeung, Fan ^a   Chung, Leland W K ^b  

^a UNIVERSITY OF VIRGINIA   (United States)

^b EMORY UNIVERSITY SCHOOL OF MEDICINE   (United States)

Author keywords

Genetic diseases; Glucocerebrosidase; Hemoglobin; Lentivirus; Retrovirus

Indexed keywords

LENTIVIRUS VECTOR; CYTOKINE; GLOBIN; GLUCOSYLCERAMIDASE;

ARTICLE; BONE MARROW DISEASE; GENE EXPRESSION; GENE TRANSFER; HEMATOPOIETIC STEM CELL; PRIORITY JOURNAL; STEM CELL; X CHROMOSOMAL INHERITANCE; ANIMAL; CELL SEPARATION; CLINICAL TRIAL; DRUG EFFECT; GENE THERAPY; GENETIC TRANSDUCTION; GENETICS; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMAN; METABOLISM; METHODOLOGY; REVIEW;

LENTIVIRUS; MURINAE; UNIDENTIFIED RETROVIRUS;

ANIMALS; BONE MARROW DISEASES; CELL SEPARATION; CLINICAL TRIALS; CYTOKINES; GENE THERAPY; GLOBINS; GLUCOSYLCERAMIDASE; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HEMATOPOIETIC STEM CELLS; HUMANS; TRANSDUCTION, GENETIC;

EID: 0036256649     PISSN: 07302312     EISSN: None     Source Type: Journal    
DOI: 10.1002/jcb.10131     Document Type: Article

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