Thérapie génique du déficit immunitaire combiné sévère lié à; l'X (DICS-X1)

Pathologie Biologie

Volumn 49, Issue 1, 2001, Pages 57-66

  Hacein Bey, S ^a   Gross, F ^a   Nusbaum, P ^a   Yvon, E ^a   Fischer, A ^a   Cavazzana Calvo, M ^a  

^a HÔPITAL NECKER ENFANTS MALADES   (France)

Author keywords

Gene therapy; Hematopoietic progenitor cells; Retroviral vector; X linked severe combined immunodeficiency (SCID X1); c chain

Indexed keywords

CD56 ANTIGEN; COMPLEMENTARY DNA; CYTOKINE RECEPTOR; HEMOGLOBIN GAMMA CHAIN; INTERLEUKIN 2; VIRUS VECTOR;

ALLOGENIC BONE MARROW TRANSPLANTATION; COMBINED IMMUNODEFICIENCY; EPSTEIN BARR VIRUS; GENE THERAPY; GENE TRANSFER; HUMAN; NATURAL KILLER CELL; PATHOGENESIS; REVIEW; STEM CELL; X CHROMOSOME LINKED DISORDER;

EID: 0035116970     PISSN: 03698114     EISSN: None     Source Type: Journal    
DOI: 10.1016/S0369-8114(00)00002-X     Document Type: Review

References (48)

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4. Long-term in vivo expression of a murine adenosine deaminase gene in rhesus monkey hematopoietic cells of multiple lineages after retroviral mediated gene transfer into CD34+ bone marrow cells
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21. - cells in cord blood and bone marrow
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39. Human CD34+ fetal liver stem cells differentiate to T cells in a mouse thymic microenvironment
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