Bone marrow gene transfer in three patients with adenosine deaminase deficiency

Gene Therapy

Volumn 3, Issue 2, 1996, Pages 179-183

  Hoogerbrugge, P M ^a   Van Beusechem, V W ^b   Fischer, A ^c   Debree, M ^c   Le Deist, F ^c   Perignon, J L ^c   Morgan, G ^d   Gaspar, B ^d   Fairbanks, L D ^e   Skeoch, C H ^f   Moseley, A ^g   Harvey, M ^g   Levinsky, R J ^d   Valerio, D ^a,b  

^a LEIDEN UNIVERSITY   (Netherlands)

^b CRUCELL HOLLAND BV   (Netherlands)

^c HÔPITAL NECKER ENFANTS MALADES   (France)

^d UNIVERSITY COLLEGE LONDON   (United Kingdom)

^e GUY S HOSPITAL   (United Kingdom)

^f ROYAL HOSPITAL FOR SICK CHILDREN   (United Kingdom)

^g Applied Immune Sciences   (United States)

Author keywords

Adenosine deaminase; Bone marrow; Gene therapy; Hemopoietic stem cell; SCID

Indexed keywords

ADENOSINE DEAMINASE; CD34 ANTIGEN;

ALLOGENIC BONE MARROW TRANSPLANTATION; ANIMAL CELL; ANIMAL EXPERIMENT; ARTICLE; CASE REPORT; CLINICAL TRIAL; COLONY FORMING CELL; COMBINED IMMUNODEFICIENCY; CONTROLLED CLINICAL TRIAL; CONTROLLED STUDY; ENZYME DEFICIENCY; GENE EXPRESSION; GENE THERAPY; GENE TRANSFER; GENETIC TRANSDUCTION; GRANULOCYTE; HEMATOPOIETIC STEM CELL; HLA MATCHING; HUMAN; HUMAN CELL; LYMPHOCYTE COUNT; MONONUCLEAR CELL; NONHUMAN; POLYMERASE CHAIN REACTION; PRESCHOOL CHILD; PRIORITY JOURNAL; RETROVIRUS; RHESUS MONKEY; STEM CELL;

ADENOSINE DEAMINASE; ANIMALS; ANTIGENS, CD34; CATTLE; DNA; GENE EXPRESSION; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HEMATOPOIETIC STEM CELLS; HUMANS; INFANT; LEUKOCYTES; MACACA MULATTA; PROVIRUSES; RETROVIRIDAE; SEVERE COMBINED IMMUNODEFICIENCY;

ADA; ANIMALIA; BOVINAE; MACACA MULATTA; UNIDENTIFIED RETROVIRUS;

EID: 9244243165     PISSN: 09697128     EISSN: None     Source Type: Journal    
DOI: None     Document Type: Article

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