Feasibility of gene therapy for late neuronal ceroid lipofuscinosis

Archives of Neurology

Volumn 58, Issue 11, 2001, Pages 1793-1798

  Sondhi, Dolan ^a   Hackett, Neil R ^a   Apblett, Robin L ^a   Kaminsky, Stephen M ^a   Pergolizzi, Robert G ^a   Crystal, Ronald G ^a  

^a WEILL CORNELL MEDICAL COLLEGE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

AMINO ACID; BETA GLUCURONIDASE; COMPLEMENTARY DNA; GENE PRODUCT; LIPOFUSCIN; MESSENGER RNA; PEPTIDASE; PROTON TRANSPORTING ADENOSINE TRIPHOSPHATE SYNTHASE; SOMATOMEDIN B RECEPTOR;

ADENO ASSOCIATED VIRUS; ADENOVIRUS; CENTRAL NERVOUS SYSTEM; GENE EXPRESSION; GENE MUTATION; GENE THERAPY; GENE TRANSFER; HUMAN; LENTIVIRINAE; NEURONAL CEROID LIPOFUSCINOSIS; NONHUMAN; PHENOTYPE; PRIORITY JOURNAL; RETINA CELL; REVIEW; STEM CELL TRANSPLANTATION;

EID: 0034762312     PISSN: 00039942     EISSN: None     Source Type: Journal    
DOI: 10.1001/archneur.58.11.1793     Document Type: Review

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