Recombinant adeno-associated virus-mediated correction of lysosomal storage within the central nervous system of the adult mucopolysaccharidosis type VII mouse

Human Gene Therapy

Volumn 11, Issue 4, 2000, Pages 507-519

  Sferra, Thomas J ^a,b,c   Qu, Guang ^a   McNeely, David ^a   Rennard, Rachel ^a   Clark, K Reed ^a,b   Lo, Warren D ^a,b   Johnson, Philip R ^a,b  

^a THE RESEARCH INSTITUTE AT NATIONWIDE CHILDREN S HOSPITAL   (United States)

^b THE OHIO STATE UNIVERSITY COLLEGE OF MEDICINE   (United States)

^c NATIONWIDE CHILDREN S HOSPITAL   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

BETA GLUCURONIDASE; VIRUS VECTOR;

ADENO ASSOCIATED VIRUS; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CENTRAL NERVOUS SYSTEM; CONTROLLED STUDY; ENZYME ACTIVITY; ENZYME ASSAY; ENZYME DEFICIENCY; GENE EXPRESSION; GENE TRANSFER; HUMAN; HUMAN CELL; LYSOSOME STORAGE DISEASE; MOUSE; MUCOPOLYSACCHARIDOSIS; NONHUMAN; NUCLEOTIDE SEQUENCE; TRANSGENE; VIRUS RECOMBINANT;

ANIMALS; BASE SEQUENCE; CENTRAL NERVOUS SYSTEM; DEPENDOVIRUS; DNA PRIMERS; FEMALE; GENE THERAPY; GENETIC VECTORS; GLUCURONIDASE; GLYCOSAMINOGLYCANS; HELA CELLS; HUMANS; LYSOSOMES; MALE; MICE; MUCOPOLYSACCHARIDOSIS VII; RECOMBINATION, GENETIC;

ADENO-ASSOCIATED VIRUS; ANIMALIA; CYTOMEGALOVIRUS; MURINAE;

EID: 0034088881     PISSN: 10430342     EISSN: None     Source Type: Journal    
DOI: 10.1089/10430340050015707     Document Type: Article

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