Myoblast gene therapy in canine mucopolysaccharidosis I: Abrogation by an immune response to α-L-iduronidase

Human Gene Therapy

Volumn 7, Issue 13, 1996, Pages 1595-1603

  Shull, Robert M ^a   Lu, Xiaochen ^a   McEntee, Michael F ^a   Bright, Ronald M ^a   Pepper, Karen A ^b   Kohn, Donald B ^b  

^a UNIVERSITY OF TENNESSEE   (United States)

^b CHILDREN S HOSPITAL LOS ANGELES   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

COMPLEMENTARY DNA; CREATINE KINASE; IMMUNOGLOBULIN G ANTIBODY; LEVO IDURONIDASE; LYSOSOME ENZYME; PLASMID DNA;

ANIMAL CELL; ANIMAL EXPERIMENT; ANTIBODY PRODUCTION; ARTICLE; CELL CULTURE; CELL INFILTRATION; CELLULAR IMMUNITY; CONTROLLED STUDY; ENHANCER REGION; ENZYME ACTIVITY; ENZYME ASSAY; ENZYME DEFICIENCY; ENZYME SYNTHESIS; GENE TARGETING; GENE THERAPY; HUMORAL IMMUNITY; HURLER SYNDROME; IMMUNE RESPONSE; INFLAMMATORY CELL; INTRAMUSCULAR DRUG ADMINISTRATION; LIVER; LYMPH NODE; MUSCLE BIOPSY; MUSCLE CELL; MYOBLAST; NONHUMAN; PLASMA CELL; POLYMERASE CHAIN REACTION; PROTEIN LOCALIZATION; SKELETAL MUSCLE; SPLEEN;

EID: 0029761477     PISSN: 10430342     EISSN: None     Source Type: Journal    
DOI: 10.1089/hum.1996.7.13-1595     Document Type: Article

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