Review of targeted treatments in fragile X syndrome

Intractable and Rare Diseases Research

Volumn 5, Issue 3, 2016, Pages 158-167

  Ligsay, Andrew ^a,b   Hagerman, Randi J ^a,c  

^a UNIVERSITY OF CALIFORNIA   (United States)

^b UNIVERSITY OF CALIFORNIA   (United States)

^c UNIVERSITY OF CALIFORNIA   (United States)

Author keywords

Clinical trials; Fragile X syndrome; Targeted treatments

Indexed keywords

4 AMINOBUTYRIC ACID RECEPTOR STIMULATING AGENT; 6 QUINOXALINECARBOXYLIC ACID PIPERIDIDE; ACAMPROSATE; ALPHA TOCOPHEROL; ARBACLOFEN; ASCORBIC ACID; BASIMGLURANT; DONEPEZIL; FRAGILE X MENTAL RETARDATION PROTEIN; LITHIUM; MAVOGLURANT; METABOTROPIC RECEPTOR 5 ANTAGONIST; METABOTROPIC RECEPTOR ANTAGONIST; METADOXINE; MEVINOLIN; MINOCYCLINE; OXYTOCIN; SEROTONIN UPTAKE INHIBITOR; SERTRALINE; TROFINETIDE; UNCLASSIFIED DRUG;

AUTISM; BEHAVIOR DISORDER; CLINICAL RESEARCH; COGNITIVE DEFECT; FRAGILE X SYNDROME; HUMAN; INTELLECTUAL IMPAIRMENT; MOLECULARLY TARGETED THERAPY; NONHUMAN; PATHOPHYSIOLOGY; PHASE 1 CLINICAL TRIAL (TOPIC); PHASE 2 CLINICAL TRIAL (TOPIC); PHASE 3 CLINICAL TRIAL (TOPIC); PHASE 4 CLINICAL TRIAL (TOPIC); RANDOMIZED CONTROLLED TRIAL (TOPIC); REVIEW;

EID: 85018234013     PISSN: 21863644     EISSN: 2186361X     Source Type: Journal    
DOI: 10.5582/irdr.2016.01045     Document Type: Review

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