Mathematical modeling of erythrocyte chimerism informs genetic intervention strategies for sickle cell disease

American Journal of Hematology

Volumn 91, Issue 9, 2016, Pages 931-937

  Altrock, Philipp M ^a,b,c   Brendel, Christian ^d   Renella, Raffaele ^a,d   Orkin, Stuart H ^a,d,e,f   Williams, David A ^a,d,f   Michor, Franziska ^a,b  

^a DANA FARBER CANCER INSTITUTE   (United States)

^b HARVARD SCHOOL OF PUBLIC HEALTH   (United States)

^c HARVARD UNIVERSITY   (United States)

^d BOSTON CHILDREN S HOSPITAL   (United States)

^e HOWARD HUGHES MEDICAL INSTITUTE   (United States)

^f HARVARD STEM CELL INSTITUTE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

BIOTIN; CD45 ANTIGEN; HEMOGLOBIN BETA CHAIN; HEMOGLOBIN F; HEMOGLOBIN GAMMA CHAIN; HEMOGLOBIN S; TRANSCRIPTION FACTOR; TRANSCRIPTION FACTOR BCL11A; UNCLASSIFIED DRUG;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; CHIMERA; ERYTHROCYTE; HEMATOPOIETIC STEM CELL; MATHEMATICAL MODEL; MOUSE; NONHUMAN; PHENOTYPE; PRIORITY JOURNAL; SICKLE CELL ANEMIA; STEM CELL GENE THERAPY;

EID: 84983050354     PISSN: 03618609     EISSN: 10968652     Source Type: Journal    
DOI: 10.1002/ajh.24449     Document Type: Article

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