Therapeutic activity of modified U1 core spliceosomal particles

Nature Communications

Volumn 7, Issue , 2016, Pages

  Rogalska, Malgorzata Ewa ^a   Tajnik, Mojca ^a   Licastro, Danilo ^b   Bussani, Erica ^a   Camparini, Luca ^a   Mattioli, Chiara ^a   Pagani, Franco ^a  

^a INTERNATIONAL CENTRE FOR GENETIC ENGINEERING AND BIOTECHNOLOGY   (Italy)

^b CBM Scrl   (Italy)

Author keywords

[No Author keywords available]

Indexed keywords

RNA; SMALL NUCLEAR RNA; SURVIVAL MOTOR NEURON PROTEIN; RNA SPLICE SITE; U1 SMALL NUCLEAR RNA;

BIOENGINEERING; CELLS AND CELL COMPONENTS; DISEASE TREATMENT; EXPERIMENTAL STUDY; MUTATION; PATHOLOGY; PROTEIN; RNA;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CONTROLLED STUDY; EXON; EXON SKIPPING; GENE MUTATION; GENE SILENCING; HUMAN; HUMAN CELL; IN VITRO STUDY; INTRON; LIFESPAN; MOUSE; MUTANT; NONHUMAN; RNA SPLICING; SPINAL MUSCULAR ATROPHY; SPLICEOSOME; SURVIVAL; ANIMAL; CHEMISTRY; CONFORMATION; GENE THERAPY; GENETICS; PATHOLOGY; PHENOTYPE; PHYSIOLOGY; RNA SPLICE SITE; TRANSGENIC ANIMAL;

ANIMALS; ANIMALS, GENETICALLY MODIFIED; GENETIC THERAPY; MICE; MUSCULAR ATROPHY, SPINAL; NUCLEIC ACID CONFORMATION; PHENOTYPE; RNA SPLICE SITES; RNA SPLICING; RNA, SMALL NUCLEAR; SPLICEOSOMES;

EID: 84962694500     PISSN: None     EISSN: 20411723     Source Type: Journal    
DOI: 10.1038/ncomms11168     Document Type: Article

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